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找到 95,669 条关于
“Microvillus Inclusion Disease”
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liver disease program
siRNA therapeutics for ocular disease/dermatological disease (Phio Pharmaceuticals)
undisclosed drug (fibrotic liver disease/NASH), Engitix/Takeda
Hereditary inclusion body myopathy gene therapy(Gradalis, Inc.)
chronic kidney disease therapy
undisclosed rare disease therapeutic (rare disease/eye disease/skin disease)
Monocyte Locomotion Inhibitory Factor (Immune Disease Institute)
Huntington's disease program (Huntington's disease)
ANTs (kidney disease/dental disease)
Lyme Disease vaccine
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