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找到 31 条关于
“NFKB1 haploinsufficiency”
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31
临床试验
15
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0
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资讯
16
去年
Pharming Group Initiates Phase II Trial of Leniolisib for Primary Immunodeficiencies
去年
NFKB1 Haplotype Predicts Improved Response to Ropeginterferon Alfa-2b in PV and ET
11个月前
CAMP4 Therapeutics Advances SYNGAP1 Gene Therapy Toward Clinical Testing with GLP Toxicology Studies
10个月前
Jaya Biosciences Secures U.S. Patent for Gene Therapy Approach to Alzheimer's Disease Treatment
7个月前
Stoke Therapeutics Initiates First-in-Human Trial of STK-002 for Rare Genetic Eye Disease ADOA
去年
Jaya Biosciences Secures Key Asian Patents for Novel Alzheimer's Gene Therapy Targeting Lysosomal Enzyme Defects
去年
TransCon hGH Meets Primary Endpoint in Turner Syndrome Trial
去年
StratosPHere 2 Trial: Evaluating Hydroxychloroquine and Phenylbutyrate for BMPR2-Related Pulmonary Hypertension
上个月
Study reveals how DNA misfolding causes congenital heart disease
去年
Alector Announces Strategic Priorities for 2025, Highlights Neurodegenerative Disease Programs
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