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找到 659 条关于
“Nonaka Myopathy”
全部
659
临床试验
491
药物
47
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43
资讯
78
5个月前
FDA Clears Ultragenyx IND Application for UX016 to Treat Rare GNE Myopathy
4个月前
Mavodelpar Shows Promise in Phase 1 Trial for Primary Mitochondrial Myopathy
6个月前
Solve GNE Advances First Gene Therapy for GNE Myopathy Toward Phase I Clinical Trial
去年
RESTEM's Restem-L Receives FDA Fast Track Designation for Idiopathic Inflammatory Myopathy
去年
Researchers Identify Two Drug Candidates for Ultra-Rare X-Linked Myopathy Using Zebrafish Model
去年
RESTEM's Restem-L Advances to Phase 2/3 Trial for Idiopathic Inflammatory Myopathy
去年
Adicet's ADI-001 CAR-T Therapy Expands Clinical Trial to Include Idiopathic Inflammatory Myopathy and Stiff Person Syndrome
去年
Cabaletta Bio to Present New CABA-201 Clinical Data at ACR Convergence 2024
去年
Adicet Bio's ADI-001 Receives FDA Clearance for Expanded Autoimmune Trial
去年
Nkarta's NKX019 Cell Therapy Trial Opens Enrollment for ANCA-Associated Vasculitis
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