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找到 21,155 条关于
“Orphan Therapeutics Accelerator”
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21,155
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5,857
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3,144
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1,151
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11,003
去年
Orphan Therapeutics Accelerator Pioneers Novel Funding Model to Rescue Ultra-Rare Disease Treatments
去年
Strategic Partnerships Transform Gene Therapy Manufacturing for Rare Diseases as Market Reaches $11.4 Billion
3年前
Elraglusib Receives FDA Orphan Drug Designation for Pancreatic Cancer Treatment
3年前
Vega Therapeutics' VGA039 Receives FDA Orphan Drug Designation for Von Willebrand Disease
去年
FDA Grants Orphan Drug Designation to Sapience Therapeutics' ST316 for Familial Adenomatous Polyposis
去年
PYC Therapeutics' VP-001 Receives FDA Orphan Drug Designation for Retinitis Pigmentosa Type 11
去年
EMA Grants Orphan Drug and ATMP Status to Capricor's Deramiocel for Duchenne Muscular Dystrophy
去年
Aileron Therapeutics Rebrands as Rein Therapeutics, Focuses on Fibrosis Therapies
2年前
FDA Grants Orphan Drug Designation to Skyline Therapeutics' SKG1108 for Retinitis Pigmentosa
去年
NUZ-001 Receives Positive Opinion for Orphan Drug Designation in Europe for ALS Treatment
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