Clinical and Molecular Description of PKD1 and PKD2 Mutation Negative Carriers in ADPKD

计划入组 1,450 人 · 首次发布于 2014 年 4 月 11 日

Polycystic Kidney Disease 1 (PKD1) Gene Variant Groups in Autosomal Dominant Polycystic Kidney Disease

计划入组 401 人 · 首次发布于 2024 年 12 月 24 日

Phase 2a Study of VX-407 in Participants With ADPKD Who Have a Subset of PKD1 Gene Variants (AGLOW)

计划入组 26 人 · 首次发布于 2025 年 9 月 8 日

MM-POD1

LAG3-PD1

PKD-003

PKD Foundation

United States

Regulus Therapeutics' Farabursen Shows Promise in ADPKD Phase 1b Trial and Gains FDA Agreement on Phase 3 Design

Novartis Acquires Regulus Therapeutics for $800M, Expanding Kidney Disease Portfolio

Helex Secures $3.5M Seed Funding to Develop Non-Viral Gene Therapy for Polycystic Kidney Disease