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找到 10,956 条关于
“Pyruvate Kinase Deficiency”
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5年前
Agios Submits New Drug Application to FDA for Mitapivat for Treatment of Adults with Pyruvate Kinase Deficiency
2年前
FDA Approves Pyrukynd as First Treatment for Pyruvate Kinase Deficiency
4年前
FDA Approves Pyrukynd (mitapivat) for Hemolytic Anemia in Adults with Pyruvate Kinase Deficiency
去年
Avanzanite Partners with Agios to Commercialize First-in-Class Pyruvate Kinase Activator Across Europe
去年
Phase 3 RISE UP Trial of Mitapivat in Sickle Cell Disease Completes Enrollment
去年
Agios' Mitapivat Receives Positive CHMP Opinion for Thalassemia Treatment in Europe
去年
Agios Pharmaceuticals Addresses Safety Concerns as PYRUKYND Receives Saudi Approval for Thalassemia
去年
Agios Pharmaceuticals Reports Strong Q3 2024 Driven by Vorasidenib Milestone and Mitapivat Progress
去年
Agios Pharmaceuticals Advances Tebapivat for Sickle Cell Disease and Hemolytic Anemias
去年
EMA Initiates Review of Rocket Pharma's Gene Therapy for Fanconi Anaemia
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