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找到 353,954 条关于
“Sanfilippo Syndrome Type A”
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353,954
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去年
Ultragenyx's UX111 Gene Therapy Shows Promise in Sanfilippo Syndrome Type A
昨天
FDA Approves Fayuvi, First-Ever Gene Therapy for Sanfilippo Syndrome Type A
去年
FDA Issues Complete Response Letter for Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A
去年
Ultragenyx's UX111 Gene Therapy for Sanfilippo Syndrome Type A Receives FDA Priority Review
4年前
Ultragenyx Acquires Global Rights to Abeona's Gene Therapy for Sanfilippo Syndrome Type A
去年
GC Biopharma and Novel Pharma Initiate Phase I Trial of GC1130A for Sanfilippo Syndrome Type A
去年
FDA Rejects Ultragenyx Gene Therapy for Sanfilippo Syndrome Over Manufacturing Concerns
2年前
JCR Pharmaceuticals' JR-441 Receives Clearance for Phase I MPS IIIA Trial in Japan
去年
FDA's START Program Selects First Rare Disease Therapies for Accelerated Development
5个月前
AAV Gene Therapy Pipeline Surpasses 250 Candidates as FDA Approvals and Late-Stage Trials Accelerate in 2026
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