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找到 97,342 条关于
“Tay Sachs disease”
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97,342
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去年
MEDIPAL Holdings and JCR Pharmaceuticals Partner on Novel GM2 Gangliosidosis Therapy JR-479
6年前
Sanofi Pivots R&D Strategy, Discontinues Diabetes Research to Focus on Novel Therapeutics
8个月前
Azafaros to Present Phase 3 Nizubaglustat Data for Rare Lysosomal Storage Disorders at WORLDSymposium 2026
3个月前
Azafaros Publishes Phase 2 RAINBOW Study Data for Nizubaglustat in GM2 Gangliosidosis and Niemann-Pick Type C Disease
去年
Florida Launches First-in-Nation Newborn Genetic Screening Program with $7.5 Million State Investment
去年
UMass Chan Gene Therapy Shows Biochemical Correction in GM2 Gangliosidosis Phase I/II Trial
去年
Myriad Genetics Launches FirstGene Multiple Prenatal Screen with Four-in-One Testing Capability
去年
Azafaros to Present at J.P. Morgan's 43rd Annual Healthcare Conference
3个月前
Florida Launches First-in-Nation Newborn Whole-Genome Sequencing Program to Detect Nearly 900 Rare Diseases
去年
Myrtelle's rAAV-Olig001-ASPA Gene Therapy Shows Promise in Canavan Disease Trial
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