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找到 2,231 条关于
“UCD”
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2,231
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236
去年
Breakthrough: First Personalized mRNA-Based CRISPR Therapy Successfully Treats Infant with Rare Metabolic Disorder
5个月前
Yeast Beta-Glucan Supplement Reprograms Bone Marrow Stem Cells to Restore Anti-Tumor Immunity in Obesity
12个月前
GENFIT Discontinues VS-01 Development in Liver Failure Following Safety Concerns, Refocuses on Rare Disease
去年
Acuitas Therapeutics and CHOP Pioneer Personalized CRISPR Therapy for Infant with Urea Cycle Disorder
6个月前
Korro Bio Advances RNA Editing Platform with KRRO-121 Nomination and $85 Million Financing
11个月前
Irish Consortium Secures €2 Million to Reduce Gene Therapy Manufacturing Costs
10个月前
Medunik USA Expands Medicaid Coverage for Pheburane in Rare Disease Treatment Access Initiative
去年
Arcturus Therapeutics to Present Phase 2 Data for ARCT-810 mRNA Therapy in Rare Genetic Disorder
11个月前
Ireland Launches Phase 2 of Precision Oncology Ireland Program with Expanded Investment and Clinical Focus
10个月前
Korro Bio's RNA Editing Drug Shows Promise but Falls Short of Efficacy Targets in Alpha-1 Antitrypsin Deficiency Trial
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