Characterizing Rate of Progression in USHer Syndrome (CRUSH) Study

计划入组 36 人 · 首次发布于 2021 年 3 月 29 日

Rate of Progression in USH2A-related Retinal Degeneration

计划入组 127 人 · 首次发布于 2017 年 5 月 9 日

A New Diagnostic Paradigm for Retinitis Pigmentosa Secondary to USH2A Pathogenic Variants

计划入组 60 人 · 首次发布于 2024 年 8 月 9 日

USH2A gene-targeting RCas13d

USH2A stereopure antisense oligonucleotide therapy

USH2A gene therapy (Usher syndrome)

AAVantgarde Bio Doses First Patient in Phase 1/2 Trial of AAVB-081 for Usher Syndrome Type 1B

Gene Editing Shows Promise for Usher Syndrome Treatment

Lyora Therapeutics Launches With $2.5M Seed Funding to Advance Genetic Medicines for Inherited Retinal Diseases