Proof of Concept Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With Duchenne Muscular Dystrophy (DMD)

计划入组 43 人 · 首次发布于 2016 年 8 月 8 日

The Use of Nutropin Depot in HIV-infected Adult Males

首次发布于 2006 年 2 月 3 日

Low Dose Growth Hormone in Obese PCOS Women

首次发布于 2007 年 8 月 21 日

utrophin expression enhancer

utrophin modulators (Summit/Sarepta)

Utrophin CRISPR/Cas9-gene therapy (University College London/Genethon)

FDA Grants Orphan Drug and Rare Pediatric Disease Designations for Duchenne Muscular Dystrophy Therapies

Ractigen's RAG-18 Receives FDA Orphan Drug Designation for Duchenne and Becker Muscular Dystrophy

Ractigen Therapeutics Initiates First-in-Human Trial of RAG-18 for Duchenne Muscular Dystrophy