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找到 42,017 条关于
“X-Linked Alport Syndrome”
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42,017
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10个月前
SonoThera Demonstrates Novel Ultrasound Gene Delivery for X-Linked Alport Syndrome Treatment
2个月前
Alport Syndrome Market Projected to Surge at 47% CAGR Through 2036, Fueled by Emerging Disease-Modifying Therapies
9个月前
Bayer Initiates Phase IIa Trial for Novel Alport Syndrome Treatment BAY 3401016
8个月前
ENYO Pharma's Vonafexor Reverses Kidney Function Decline in Phase 2 Alport Syndrome Trial
上个月
Eloxx Pharmaceuticals Strengthens Balance Sheet with $66 Million Offering, Advances Exaluren Toward Phase 2b in Alport Syndrome
2年前
FDA Grants Orphan Drug and Rare Pediatric Disease Designations to ATSN-201 for X-Linked Retinoschisis
2年前
Two Major Breakthroughs in Fragile X Syndrome Treatments
9个月前
Mirum Pharmaceuticals Initiates Phase II Trial of MRM-3379 for Fragile X Syndrome
2年前
FDA Grants Orphan Drug Status to Spinogenix's SPG601 for Fragile X Syndrome
4个月前
FDA Approves Enhanced Dosing Options for CRYSVITA in Adults with X-linked Hypophosphatemia
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