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找到 13,324 条关于
“X-linked myotubular myopathy”
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13,324
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8,982
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783
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85
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3,474
去年
Astellas Discontinues DMD Gene Therapy Programs, Takes $170M Impairment Charge
去年
Researchers Identify Two Drug Candidates for Ultra-Rare X-Linked Myopathy Using Zebrafish Model
2年前
FDA Grants Orphan Drug and Rare Pediatric Disease Designations to ATSN-201 for X-Linked Retinoschisis
10个月前
SonoThera Demonstrates Novel Ultrasound Gene Delivery for X-Linked Alport Syndrome Treatment
9个月前
Beacon Therapeutics Initiates LANDSCAPE Trial for X-Linked Retinitis Pigmentosa Gene Therapy
4个月前
FDA Approves Enhanced Dosing Options for CRYSVITA in Adults with X-linked Hypophosphatemia
去年
FDA Grants RMAT Designation to Gene Therapies for Retinitis Pigmentosa
去年
Phase 2 SKYLINE Trial Shows Promising Results for Gene Therapy in X-Linked Retinitis Pigmentosa
去年
Beacon Therapeutics Reports Promising Phase 2 Data for Gene Therapy in X-Linked Retinitis Pigmentosa
5个月前
MeiraGTx Reacquires Gene Therapy Botaretigene Sparoparvovec from Johnson & Johnson for X-linked Retinitis Pigmentosa Treatment
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