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找到 6,940 条关于
“antisense oligonucleotide (ASO)”
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6,940
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3,367
去年
Vanda Pharmaceuticals' VGT-1849A, a Selective JAK2 Inhibitor, Receives FDA Orphan Drug Designation for Polycythemia Vera
3个月前
ASO Targeting ZFP384 Sustains Microglial Repair Activity and Extends Stroke Recovery Window
去年
QurAlis Secures Exclusive License for Novel RNA-Targeted Therapy in Fragile X Syndrome
去年
Ionis Pharmaceuticals' ION582 Receives FDA Fast Track Designation for Angelman Syndrome Treatment
10个月前
Aperture Therapeutics Advances CD33-Targeting Antisense Oligonucleotide APRTX-001 for Neurodegenerative Diseases
去年
Sarepta Therapeutics Halts Development of Vesleteplirsen for Duchenne Muscular Dystrophy
2年前
Viva's Portfolio Companies Announce Significant Advances in Biopharmaceutical Innovations
去年
SynaptixBio Selects Antisense Oligonucleotide Candidate for Rare Disease H-ABC Clinical Trials
去年
AusperBio Secures $73 Million to Advance Chronic Hepatitis B Therapy
11天前
Aptar and Aceso Therapeutics Partner to Advance Inhaled Antisense Oligonucleotide Therapy for Cystic Fibrosis
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