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找到 3,573 条关于
“autosomal recessive osteopetrosis”
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去年
Scientists Discover Critical Window for In Vivo Gene Therapy in Newborns
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Biallelic EHMT2 Variants Identified in Second-Ever Case of Autosomal Recessive Kleefstra-Like Neurodevelopmental Syndrome
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āshibio Licenses Vantictumab for Rare Bone Disease ADO2 in Strategic Pipeline Expansion
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Genetics of Parkinson Disease: Paradigm Shifts and Future Prospects
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GSK Receives FDA Orphan Drug Designation for Autosomal Dominant Polycystic Kidney Disease Treatment
11个月前
Calico's ABBV-CLS-628 Receives FDA Fast Track Designation for Autosomal Dominant Polycystic Kidney Disease
去年
Gene Editing Shows Promise for Treating Autosomal Dominant Hearing Loss
去年
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2年前
ViGeneron Doses First Patient in Phase 1b Clinical Trial of VG901 for Retinitis Pigmentosa Treatment
去年
Quince Therapeutics' EryDex Phase 3 Trial for Ataxia-Telangiectasia Nears Enrollment Completion
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