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找到 7,452 条关于
“dual AAV8.ABCA4”
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7,452
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2,773
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去年
AAVantgarde to Present Promising Gene Therapy Data for Usher 1B and Stargardt Disease at ARVO 2025
去年
SpliceBio Initiates First-in-Human Trial of Dual AAV Gene Therapy for Stargardt Disease
去年
Ocugen's OCU410ST Receives Orphan Drug Designation from EMA for ABCA4 Retinopathies
8个月前
SpliceBio Advances Gene Therapy for Stargardt Disease with First Patient Dosed in Phase 1/2 Expansion Trial
5个月前
AAVantgarde Presents Interim LUCE-1 Trial Data for Usher Syndrome 1B Gene Therapy at ARVO 2026
去年
Ocugen's OCU410ST Receives EMA Orphan Drug Designation for ABCA4-Associated Retinopathies
去年
Ocugen's OCU410ST Receives EMA Orphan Drug Designation for ABCA4-Associated Retinopathies
去年
EMA Grants Orphan Drug Designation to Ocugen's OCU410ST for ABCA4-Associated Retinopathies
去年
AAVantgarde Bio Doses First Patient in Phase 1/2 Trial of AAVB-081 for Usher Syndrome Type 1B
去年
SpliceBio Raises $135 Million Series B to Advance First Dual AAV Gene Therapy for Stargardt Disease
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