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找到 1,986 条关于
“familial dysautonomia”
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1,986
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1,698
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264
去年
FDA Awards Dual Designations to Tikun's Novel Familial Dysautonomia Treatments
去年
FDA Expands Rare Disease Research Support with $27 Million in Grants and New Innovation Hub
去年
Homozygous Familial Hypercholesterolemia Treatment Market to Surge by 2034
去年
Comprehensive Treatment Options Expand for Non-Familial Hypercholesterolemia Management
2年前
Maralixibat Demonstrates Efficacy in Treating Pruritus and Reducing Bile Acids in PFIC Patients
去年
Japanese Researchers Launch Final Phase Trial of Bromocriptine for Familial Alzheimer's Disease
6个月前
FDA Approves Juxtapid for Pediatric Patients with Homozygous Familial Hypercholesterolemia
去年
Esperion Advances Bempedoic Acid to Phase 3 Trials for Pediatric Familial Hypercholesterolemia
去年
Arrowhead Submits FDA Application for Plozasiran in Familial Chylomicronemia Syndrome
去年
Novartis Secures Pan-Canadian Agreement for Leqvio Access in Familial Hypercholesterolemia
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