Safety and Efficacy of CRISPR/Cas9 mRNA Instantaneous Gene Editing Therapy to Treat Refractory Viral Keratitis

计划入组 3 人 · 首次发布于 2020 年 9 月 23 日

CRISPR/Cas9 Instantaneous Gene Editing Therapy to Intraocular Hypertensive POAG With MYOC Mutation

计划入组 9 人 · 首次发布于 2024 年 6 月 20 日

An Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its Long-Lasting Effects in DMD Patients (MUSCLE)

计划入组 4 人 · 首次发布于 2024 年 9 月 19 日

TTR gene editing therapy (Trucode Gene)

CYBB gene editing therapy (Trucode Gene)

PAH gene editing therapy (Trucode Gene)

CELL AND GENE THERAPY CATAPULT

United Kingdom

JIUYUAN GENE

Triple-Gene LLC

United States

CRISPR Gene Editing Shows Promise in Hereditary Angioedema

NTLA-2002 Gene Editing Shows Promise in Hereditary Angioedema

Breakthrough Gene Editing Therapy Successfully Treats Infant with Rare Metabolic Disorder