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找到 87,967 条关于
“gene replacement therapy”
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87,967
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上个月
Genezen and Raiden Science Foundation Partner to Advance First AAV9 Gene Replacement Therapy for UBA5 Disorder Toward Clinical Trial
去年
UC Davis Health Premieres Documentary on Duchenne Muscular Dystrophy Gene Therapy Trial
去年
Nuevocor Receives FDA IND Clearance for Gene Therapy Targeting Rare Genetic Heart Disease
去年
FDA Approves PTC Therapeutics' Kebilidi, First Gene Therapy with Direct Brain Administration for AADC Deficiency
3个月前
In Utero Gene Therapy Approaches First FDA Trial After 25 Years of Development
去年
FDA Approves KEBILIDI, First Brain-Delivered Gene Therapy for AADC Deficiency
9个月前
FDA Approves First Intrathecal Gene Therapy for Spinal Muscular Atrophy Across All Ages
9个月前
FDA Approves Novartis Gene Therapy Itvisma for Spinal Muscular Atrophy in Older Patients
去年
First Patient Receives Gene Therapy for Ultra-Rare NEDAMSS Disease in Record 13-Month Timeline
4个月前
Novartis Receives Positive CHMP Opinion for Itvisma Gene Therapy for Spinal Muscular Atrophy
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