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找到 45,963 条关于
“genetic neuromuscular disorder”
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45,963
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去年
Neucore Bio Receives $350K NIH Grant to Develop Exosome-Based Gene Therapy for Charcot-Marie-Tooth Disease
去年
First-in-Human Gene Therapy Trial Launches for Rare Muscle Disorder FSHD
去年
FDA Accepts Scholar Rock's BLA for Apitegromab in Spinal Muscular Atrophy with Priority Review
9个月前
Agora Open Science Trust Selects M4K2009 as Lead Candidate for Rare Pediatric Brain Cancer Treatment
去年
Edgewise Therapeutics Announces 2025 Priorities Following Positive Phase 2 Results
3个月前
OpenAI's o3 Model Helps Boston Children's Hospital Diagnose 18 Children with Rare Diseases That Had Eluded Experts
9个月前
Merck's Cladribine Capsules Receive FDA Fast Track Designation for Rare Neuromuscular Disorder
去年
Andelyn Biosciences Partners with Amplo Biotechnology to Advance AAV Gene Therapies for Neuromuscular Junction Disorders
去年
ARTHEx Biotech Secures $87M Series B to Advance Novel RNA Therapy for Myotonic Dystrophy Type 1
去年
Key Advances in Neuromuscular and Movement Disorder Treatments Highlighted in 2024
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