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找到 88,788 条关于
“genetic skin diseases”
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去年
Kamari Pharma Secures $23 Million Series A to Advance First-in-Class TRPV3 Inhibitor for Rare Genetic Skin Diseases
去年
Palvella Therapeutics Advances QTORIN™ Rapamycin for Rare Genetic Skin Diseases
4个月前
LEO Pharma Acquires Replay for $50 Million to Advance HSV Gene Therapy Platform for Rare Skin Diseases
去年
Palvella Therapeutics Gains Analyst Attention with QTORIN Rapamycin Development for Rare Skin Diseases
7个月前
First Topical CRISPR Gene Therapy Successfully Corrects Disease-Causing Mutations in Human Skin
去年
Palvella Therapeutics Appoints Rare Disease Commercial Expert Ashley Kline as Chief Commercial Officer
5个月前
Orvida Pharma Reports Positive Phase 1a Safety Data for KM-023, First-in-Class TRPV3 Inhibitor for Olmsted Syndrome
3年前
Palvella Therapeutics Announces Positive Topline Results from Phase 2 Study for Microcystic Lymphatic Malformations
去年
Palvella Therapeutics Doses First Patient in Phase 3 Trial of QTORIN™ Rapamycin for Microcystic Lymphatic Malformations
去年
Palvella Therapeutics Receives FDA Grant for Phase 3 Trial of QTORIN Rapamycin in Microcystic Lymphatic Malformations
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