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找到 7,962 条关于
“hemoglobin beta-globin”
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7,962
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5个月前
EpiFrontier Therapeutics Secures $32M AMED Grant to Advance First-in-Class G9a Inhibitor for Beta Globin Disorders
去年
Tessera Therapeutics Reports Breakthrough Gene Editing Results for Multiple Genetic Diseases
去年
Kanglin Biotechnology Secures $20 Million to Advance KL003 Gene Therapy for Beta Thalassemia and Sickle Cell Disease
去年
YolTech Therapeutics Launches Clinical Trial for In Vivo Gene Editing Therapy YOLT-204 in Transfusion-Dependent Beta-Thalassemia
6个月前
Lonza and Genetix Extend Manufacturing Partnership for ZYNTEGLO Gene Therapy Amid Rising Patient Demand
3年前
Editas Medicine Advances EDIT-301 for Sickle Cell Disease and Beta Thalassemia, Prioritizes In Vivo Gene Editing
去年
EMA Approves Bluebird Bio's Zynteglo, First Gene Therapy for Beta Thalassemia
去年
CRISPR-Based Casgevy Emerges as Preferred Gene Therapy for Beta-Thalassemia, Survey Shows
去年
Beam Therapeutics Receives FDA Orphan Drug Designation for BEAM-101 Sickle Cell Disease Therapy
去年
Cellarity Initiates Phase 1 Trial of CLY-124, First-in-Class Oral Therapy for Sickle Cell Disease
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