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找到 8,155 条关于
“hereditary antithrombin deficiency”
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8,155
临床试验
6,619
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190
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6
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1,340
10个月前
FDA Approves First Antithrombin Concentrate for Pediatric Patients with Hereditary Antithrombin Deficiency
去年
Fitusiran Demonstrates Efficacy in Hemophilia A and B with Reduced Factor Consumption
去年
NTLA-2002 Demonstrates Significant Reduction in Angioedema Attacks via CRISPR-Cas9 Gene Editing
去年
FDA Accepts Donidalorsen NDA for Hereditary Angioedema Prophylaxis
去年
BioCryst's Orladeyo Demonstrates Safety and Efficacy in Pediatric Hereditary Angioedema Trial
5年前
Agios Submits New Drug Application to FDA for Mitapivat for Treatment of Adults with Pyruvate Kinase Deficiency
去年
FDA Grants Orphan Drug Designation to COAGADEX for Rare Bleeding Disorder Associated with AL Amyloidosis
去年
FDA Delays Sebetralstat Approval Decision for Hereditary Angioedema Treatment Due to Resource Constraints
去年
FDA Approves Larger Vial Sizes of Takeda's GLASSIA for Alpha-1 Antitrypsin Deficiency
去年
KalVista's Sebetralstat Halts Hereditary Angioedema Attacks in Median 19.8 Minutes Across Clinical Trials
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