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找到 19,864 条关于
“hereditary inclusion body myopathy”
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19,864
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14,474
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119
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30
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5,241
5个月前
FDA Clears Ultragenyx IND Application for UX016 to Treat Rare GNE Myopathy
10个月前
Novel Gene Therapy AVGN7.2 Shows Promising Safety Profile in Preclinical Study for Inclusion Body Myositis
7个月前
Abcuro's Ulviprubart Misses Primary Endpoints in Inclusion Body Myositis Trial, Shows Promise in Mild-to-Moderate Patients
去年
RESTEM's Restem-L Receives FDA Fast Track Designation for Idiopathic Inflammatory Myopathy
去年
New NMOSD Treatment Recommended for PBS Inclusion
4个月前
Mavodelpar Shows Promise in Phase 1 Trial for Primary Mitochondrial Myopathy
6个月前
Solve GNE Advances First Gene Therapy for GNE Myopathy Toward Phase I Clinical Trial
7个月前
Klotho Neurosciences Secures Australian Patent for Novel Gene Therapy Targeting Motor Neuron Diseases
去年
Researchers Identify Two Drug Candidates for Ultra-Rare X-Linked Myopathy Using Zebrafish Model
去年
CHOP Researchers Propose ALK Inhibitors as New Standard for Hereditary Neuroblastoma
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