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找到 32 条关于
“homocystinuria”
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32
临床试验
22
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3
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资讯
7
去年
Travere Therapeutics Pauses Enrollment in Phase 3 Homocystinuria Trial Due to Manufacturing Issues
去年
Travere Therapeutics Pauses Enrollment in Phase 3 Pegtibatinase Trial for Homocystinuria Due to Manufacturing Issues
8个月前
Travere Therapeutics Reports Record FILSPARI Sales and Prepares for FSGS Approval Decision
去年
Synlogic's Novel Probiotic Therapy Shows Promise in Phase 2 PKU Trial, Advancing to Phase 3
去年
Sidra Medicine Launches Clinical Trials Program for Rare Pediatric Diseases in the Arab Region
去年
Sidra Medicine Conducts First Clinical Trial for Pediatric Congenital Hyperinsulinism
去年
Breakthrough Gene Editing Therapy Successfully Treats Infant with Rare Metabolic Disorder