Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I

计划入组 6 人 · 首次发布于 2014 年 9 月 5 日

Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease

计划入组 3 人 · 首次发布于 2005 年 11 月 24 日

Clinical Study of Aldurazyme in Patients With Mucopolysaccharidosis (MPS) I

计划入组 45 人 · 首次发布于 2009 年 6 月 3 日

iduronidase alpha-lectin fusion protein

DNL-622

Alpha-L-iduronidase gene therapy (Christie Hospital)

Immusoft's Engineered B-Cell Therapy Shows Promise in MPS I Trial

Immusoft Reports Breakthrough Results from First-Ever Engineered B Cell Therapy in MPS I Clinical Trial

JCR Pharmaceuticals' Laronidase for Hurler Syndrome Expected to Generate $38M by 2040