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找到 3,081 条关于
“leber congenital amaurosis”
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3,081
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6年前
First In Vivo CRISPR Therapy Dosed in Clinical Trial for Congenital Blindness
去年
HuidaGene's CRISPR/Cas13 RNA-Editing Therapy HG202 Cleared for US Trial in Macular Degeneration
去年
Ocugen to Highlight Retinal Gene Therapy Progress at Clinical Showcase
2年前
Gene Therapy Shows Promise in Restoring Vision for LCA1 Patients
去年
Hubble Therapeutics Secures $7.3M Series A Funding for Gene Therapy Targeting Rare Childhood Blindness
去年
MeiraGTX's Gene Therapy Shows Promising Visual Benefits in Children with Rare Genetic Blindness
去年
Children's Hospital Los Angeles Celebrates Milestone with 100th Retinal Gene Therapy Procedure
去年
FDA Approves Autolus' Obecabtagene Autoleucel (Aucatzyl) for R/R B-cell ALL
2年前
CRISPR Gene Editing Shows Promise in Treating Rare Form of Blindness
5个月前
Philadelphia Scientists Win $3 Million Breakthrough Prize for First FDA-Approved Gene Therapy for Inherited Blindness
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