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找到 1,032 条关于
“lyso-Gb3”
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1,032
临床试验
690
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280
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2
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60
去年
Elfabrio Shows Promise in Phase 3 BRIGHT Study for Fabry Disease
去年
uniQure's AMT-191 Gene Therapy Shows Sustained Enzyme Activity and ERT Discontinuation in Fabry Disease Phase I/IIa Trial
去年
Less Frequent Elfabrio Dosing Shows Promise in Fabry Disease
去年
AceLink Therapeutics' AL01211 Shows Promising Safety and Biomarker Reduction in Phase 2 Fabry Disease Trial
去年
Sangamo's Gene Therapy Shows Sustained Benefits in Fabry Disease Patients with Improved Kidney Function
10个月前
Sangamo Therapeutics Advances Fabry Disease Gene Therapy Toward FDA Submission Following Positive Clinical Data
去年
Spur Therapeutics' FLT201 Gene Therapy Shows Promise in Gaucher Disease with FDA Alignment on Phase 3
8个月前
Lucerastat Demonstrates Significant Efficacy in Phase 3 Trial for Fabry Disease Treatment
8个月前
Spur Therapeutics to Present Two-Year Clinical Data for FLT201 Gene Therapy in Gaucher Disease at WORLDSymposium
2年前
4DMT's 4D-310 Shows Promising Cardiac Improvements in Fabry Disease Trial
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