PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

计划入组 10 人 · 首次发布于 2020 年 8 月 31 日

Selected Lysosomal Enzyme Activities and the Oxidant-antioxidant Balance in Hyperbaric Oxygen Condition.

计划入组 78 人 · 首次发布于 2024 年 5 月 7 日

Scripps Genomics Health Initiative

计划入组 10,000 人 · 首次发布于 2008 年 12 月 16 日

lysosomal enzyme allosteric regulator program

Digestive Enzyme

Rx

enzyme inhibitor (PHD Biosciences)

AMANO ENZYME INC.

Japan

LYSOSOMAL AND RARE DISORDERS RESEARCH AND TREATMENT CENTER, INC.

United States

Reneo Pharmaceuticals

United States

Jaya Biosciences Secures Key Asian Patents for Novel Alzheimer's Gene Therapy Targeting Lysosomal Enzyme Defects

Jaya Biosciences Secures U.S. Patent for Gene Therapy Approach to Alzheimer's Disease Treatment

2024 Breakthroughs and Setbacks in Lysosomal Disorder Gene Therapies