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找到 46,553 条关于
“metabolic disorder”
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46,553
临床试验
40,634
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356
机构
52
资讯
5,511
去年
Breakthrough Gene Editing Therapy Successfully Treats Infant with Rare Metabolic Disorder
去年
CRISPR Gene Editing Breakthrough Saves Baby with Ultra-Rare Metabolic Disorder
去年
First Infant Successfully Treated with Novel Gene Therapy for Rare Metabolic Disorder
10个月前
FDA Approves First siRNA Therapy Plozasiran for Rare Metabolic Disorder Familial Chylomicronemia Syndrome
9个月前
First-Ever Personalized CRISPR Therapy Successfully Treats Baby with Ultra-Rare Metabolic Disorder
去年
Breakthrough: First Personalized mRNA-Based CRISPR Therapy Successfully Treats Infant with Rare Metabolic Disorder
去年
FDA Approves First Treatment for Alkaptonuria: Nitisinone Shows Clinical Benefits in Rare Metabolic Disorder
5个月前
FDA Clears IND for Gene Therapy Candidate MMA-101 to Treat Rare Metabolic Disorder Methylmalonic Acidemia
去年
NIH to Advance Gene Therapy Trial for Rare Metabolic Disorder After Biotech Pullout
11个月前
NIH Awards $15.6 Million to Advance Research on Rare Bone and Metabolic Disorders
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