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找到 8,321 条关于
“mucopolysaccharidosis IVA”
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8,321
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去年
FDA Grants Rare Pediatric Disease and Orphan Drug Designations to Six Gene Therapies
11年前
NICE Provisionally Approves BioMarin's Vimizim for Ultra-Rare Morquio Disease with Real-World Data Requirements
去年
NICE Recommends Vanzacaftor-Tezacaftor-Deutivacaftor for Cystic Fibrosis Treatment in England
2年前
JCR Pharmaceuticals' JR-441 Receives Clearance for Phase I MPS IIIA Trial in Japan
去年
NRG258 Trial: Chemoradiation Fails to Improve Overall Survival in Advanced Endometrial Cancer
去年
European Commission Approves Pembrolizumab Regimens for Endometrial and Cervical Cancers
去年
Novel Therapies and Combinations Lead the Way in Women's Cancers in 2024
18天前
Inventiva Appoints Chris Benecchi as Chief Operating Officer Ahead of Pivotal MASH Phase 3 Readout
2年前
Pembrolizumab Plus Chemoradiotherapy Significantly Improves Overall Survival in Advanced Cervical Cancer
2年前
KEYTRUDA Plus Chemoradiotherapy Improves Overall Survival in High-Risk Cervical Cancer
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