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找到 36,807 条关于
“nonsense mutation Alport syndrome”
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36,807
临床试验
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上个月
Eloxx Pharmaceuticals Strengthens Balance Sheet with $66 Million Offering, Advances Exaluren Toward Phase 2b in Alport Syndrome
2个月前
Alport Syndrome Market Projected to Surge at 47% CAGR Through 2036, Fueled by Emerging Disease-Modifying Therapies
9个月前
Bayer Initiates Phase IIa Trial for Novel Alport Syndrome Treatment BAY 3401016
去年
FDA Accepts Resubmission of Translarna NDA for Nonsense Mutation Duchenne Muscular Dystrophy
2年前
FDA Accepts PTC Therapeutics' Translarna NDA Resubmission for Nonsense Mutation Duchenne Muscular Dystrophy
10个月前
SonoThera Demonstrates Novel Ultrasound Gene Delivery for X-Linked Alport Syndrome Treatment
8个月前
ENYO Pharma's Vonafexor Reverses Kidney Function Decline in Phase 2 Alport Syndrome Trial
去年
FDA Accepts Resubmitted NDA for Ataluren in Nonsense Mutation Duchenne Muscular Dystrophy
2个月前
Li-Fraumeni Syndrome: The TP53 Mutation That Confers Nearly 100% Lifetime Cancer Risk
12个月前
DEBRA Research and Nonsense Therapeutics Form ReadOn Therapeutics to Advance Epidermolysis Bullosa Treatments
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