Ornithine carbamoyltransferase deficiency disease therapeutics (iECURE)

Ornithine(Primene)

C₅H₁₂N₂O₂

N-(Phosphonoacetyl)-L-Ornithine

C₇H₁₅N₂O₆P

L-Ornithine-L-Aspartate

Rx

Ndelta-(N'-Sulphodiaminophosphinyl)-L-Ornithine

C₅H₁₅N₄O₆PS

MNK-6105

N(5)-[(hydroxyamino)(imino)methyl]-L-ornithine

C₆H₁₄N₄O₃

OTC gene therapy (eRNA/LNP, ornithine transcarbamylase deficiency)

N(G)-Iminoethylornithine

C₇H₁₅N₃O₂

Avalotcagene ontaparvovec