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找到 6,885 条关于
“ornithine transcarbamylase deficiency”
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6,885
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去年
Arcturus Therapeutics Initiates Phase 2 Trials for mRNA Therapies Targeting Cystic Fibrosis and OTC Deficiency
去年
Arcturus Therapeutics Poised for Growth with Cystic Fibrosis and OTCD Therapies
去年
Precision BioSciences' ARCUS Platform Shows Promising Clinical Outcomes in Gene Editing Trial
去年
Arcturus Therapeutics to Present Phase 2 Data for ARCT-810 mRNA Therapy in Rare Genetic Disorder
去年
Arcturus Therapeutics' COVID-19 Vaccine Kostaive Receives Positive EMA Recommendation
2年前
Ultragenyx Announces Preliminary 2023 Revenue and 2024 Financial Guidance
去年
Arcturus Therapeutics Advances mRNA Pipeline and Reports Q3 2024 Financial Results
去年
iECURE's Gene Insertion Therapy ECUR-506 Shows Complete Clinical Response in OTC Deficiency Trial
3个月前
Arcturus Therapeutics Advances mRNA Pipeline with Multiple Phase 2 Rare Disease Programs and Self-Amplifying RNA Vaccine Platform
11个月前
UK's Innovative Licensing and Access Pathway Awards First Innovation Passports to Three Rare Disease Therapies
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