Sapropterin(Javygtor, Kuvan, Sapropterin Dipharma)

C₉H₁₅N₅O₃ · Rx

iECURE-PKU

AP-308

Phenylketonuria(Exegenesis Bio)

Phenylketonuria Therapy (Pluvia)

Phenylketonuria (Stemirna Therapeutics)

Phenylketonuria Therapeutics (iECURE)

Phenylketonuria(Tome Biosciences)

PKU program(IEcure, Inc.)

ERα PROTAC(PKU Shenzhen)