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找到 117,301 条关于
“rare genetic disease”
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117,301
临床试验
91,010
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538
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24,154
去年
Adenine Base Editing Shows Promise in X-Linked Chronic Granulomatous Disease Trial
9个月前
Arrowhead Pharmaceuticals Soars 23% on FDA Approval of REDEMPLO for Rare Genetic Disease
去年
Arnatar Therapeutics Emerges with $52M to Develop First-in-Class RNA Therapy for Rare Genetic Disease
去年
Corvus Pharmaceuticals Initiates Phase 2 Trial of Soquelitinib for Rare Genetic Disease ALPS
2个月前
Illumina Launches TruPath Genome, a $395 Whole-Genome Workflow Targeting Rare Genetic Disease
去年
Kamari Pharma Secures $23 Million Series A to Advance First-in-Class TRPV3 Inhibitor for Rare Genetic Skin Diseases
2个月前
Rapid Whole-Genome Sequencing Cuts Severe Neonatal Rare Disease Diagnosis From 5 Years to 5.5 Days
2个月前
OXB Selected as GMP Manufacturing Partner for Plowshare Therapies' AAV Gene Therapy Programme Targeting Rare Genetic Diseases
去年
Can-Fite Advances Piclidenoson to Phase II Trial for Rare Lowe Syndrome with No Current Treatments
去年
Revolutionary Blood Test Promises Rapid Diagnosis for Thousands of Rare Genetic Diseases in Children
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