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找到 69,814 条关于
“rare genetic disorders”
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69,814
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去年
Matica Biotechnology Partners with Childs Cure to Develop Gene Therapy for Rare Genetic Disorders
5个月前
Vosoritide Shows Promise for Rare Genetic Growth Disorders Beyond Achondroplasia in Phase 2 Trial
10个月前
Five Major FDA Decisions Expected in November 2025 Across Cancer, Rare Disease, and Genetic Disorders
2个月前
Texas Children's Physician-Scientist Wins $700,000 Burroughs Wellcome Fund Award to Uncover Genetic Drivers of Rare Immune Disorders
去年
FDA Aligns with Gemini Therapeutics on APOLLO Trial Design for Bitopertin in Rare Porphyria Disorders
去年
Clinical Trial Offers New Hope for Child with Rare Genetic Disorder
去年
Yale Researchers Repurpose Cancer Drug Erlotinib for Rare Genetic Skin Disorder
去年
First-of-its-kind Gene Editing Treatment Saves Baby with Rare Genetic Disorder
去年
Vanda Pharmaceuticals Initiates First-in-Human Trial of Personalized ASO Therapy VCA-894A for Ultra-Rare CMT2S
去年
FDA Grants RMAT Designation to Elixirgen's Novel Gene Therapy for Rare Telomere Disorders
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