Ceritinib Rare Indications Study in ALK+ Tumors

计划入组 22 人 · 首次发布于 2015 年 6 月 8 日

Expanded Indications in the Pediatric BONEBRIDGE Population

计划入组 36 人 · 首次发布于 2022 年 11 月 14 日

DETERMINE (Determining Extended Therapeutic Indications for Existing Drugs in Rare Molecularly Defined Indications Using a National Evaluation Platform Trial) - Master Screening Protocol

计划入组 825 人 · 首次发布于 2023 年 2 月 10 日

undisclosed pediatric rare disease program (rare CNS diseases)

undisclosed pediatric rare disease therapeutic (rare disease/kidney disease)

undisclosed pediatric rare disease therapeutic (rare disease/immune disease)

RTA Pediatric Care Inc.

United States

Landon Pediatric Foundation

United States

Halton Pediatric Allergy

Canada

Cumberland Pharmaceuticals' Ifetroban Advances Across Multiple Rare Disease Indications

Oncotelic Therapeutics Advances Clinical Pipeline Led by CEO's $4.2B Patent Legacy

FDA Expands Methotrexate Approval to Include Pediatric ALL and pJIA