Safety and Efficacy Evaluation of ET-01 Transplantation in Subjects With Transfusion Dependent β-Thalassaemia

计划入组 3 人 · 首次发布于 2020 年 5 月 18 日

A Study to Evaluate the Safety and Efficacy of ET-01 Transplantation in Subjects with Transfusion Dependent Β-Thalassaemia.

计划入组 2 人 · 首次发布于 2023 年 3 月 2 日

A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia

计划入组 8 人 · 首次发布于 2021 年 6 月 14 日

Effectiveness of hydroxyurea treatment compared to placebo in reducing transfusions in beta-thalassaemia patients.

Efficacy and safety of triple iron chelator (deferoxamine, deferasirox, and deferiprone) versus dual iron chelator (deferoxamine and deferasirox) combination therapy for reducing iron overload in transfusion-dependent beta-thalassaemia with very high iron overload.

Efficacy and Safety Study of Multiple Doses of VIT-2763 in Adults With Transfusion-dependent Beta-thalassemia

首次发布于 2021 年 6 月 24 日

A study to evaluate if VIT-2763 may be beneficial in the treatment of Nontransfusion Dependent Beta-thalassaemia.

计划入组 25 人

Study in Beta-thalassaemia or Myelodysplastic Syndrome Patients to Investigate the Safety and Tolerability of SLN124

首次发布于 2019 年 11 月 25 日

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

计划入组 10 人 · 首次发布于 2024 年 10 月 18 日

Gene Therapy for Transfusion Dependent Beta-thalassemia

计划入组 10 人 · 首次发布于 2015 年 5 月 25 日