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找到 411 条关于
“utrophin”
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411
临床试验
392
药物
7
机构
0
资讯
12
2年前
FDA Grants Orphan Drug and Rare Pediatric Disease Designations for Duchenne Muscular Dystrophy Therapies
2年前
Ractigen's RAG-18 Receives FDA Orphan Drug Designation for Duchenne and Becker Muscular Dystrophy
9个月前
Ractigen Therapeutics Initiates First-in-Human Trial of RAG-18 for Duchenne Muscular Dystrophy
去年
Summit Therapeutics' Phase 3 HARMONi Trial Poised for Mid-2025 Readout in Duchenne Muscular Dystrophy
上个月
Ractigen Therapeutics Closes $31M+ Financing to Advance saRNA Pipeline and Extrahepatic Delivery Platforms
2年前
Solid Biosciences Tracks Long-Term Cardiac Effects of SGT-001 Gene Therapy for Duchenne Muscular Dystrophy
4年前
Efficacy and Safety of Elian Granules in Treating Chronic Atrophic Gastritis
2年前
Houtou Jianweiling Tablet Shows Promise in Treating Chronic Non-Atrophic Gastritis
2年前
Efficacy and Safety of Piwei Peiyuan Prescription in Treating Chronic Atrophic Gastritis
3个月前
OCT Biomarkers Distinguish Progression to Neovascular vs. Atrophic AMD in Intermediate Disease
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