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Cardiac Amyloidosis Registry of University Hospital Leipzig

Recruiting
Conditions
Cardiac Amyloidosis
Interventions
Other: Routine diagnostics
Other: Routine treatment
Registration Number
NCT06129656
Lead Sponsor
University of Leipzig
Brief Summary

This is a clinical registry of patients with cardiac amyloidosis being treated at University Hospital Leipzig. The aim of the registry is to collect detailed information about clinical events, symptoms, imaging, biomarkers, comorbidities, and treatment from routine patient management which would not be provided by randomized clinical trails.

Detailed Description

Cardiac amyloidosis is increasingly diagnosed since awareness of the disease and therapeutic options increase. There is evidence from clinical trials about warning signs ("red flags"), diagnostic algorithms, and evidence for specific treatment. However, patients in randomized clinical studies are highly selected and do not necessarily reflect clinical practise. Furthermore, large clinical trials do not account for national medical care differences nor provide data about long-term outcome and the associations with comorbidities.

Clinical registries may reflect broad clinical practise and help to characterize cardiac amyloidosis in terms of epidemiology, application of diagnostic methods, the impact of comorbidities, and real-world clinical course. Furthermore, clinical registry studies may validate data from randomized clinical trials, provide information on implementation of treatment, the quality of interventions, monitoring patients during treatment, and inform about the safety of procedures.

The cardiac amyloidosis registry aims to collect data from the routine clinical management of patients with cardiac amyloidosis at the tertiary care University Hospital Leipzig. In particular, obtaining data about clinical events of heart disease, hemodynamic measures from echocardiography and circulation biomarkers, cardiac morphology from different imaging methods, clinical status, functional capacity, quality of life, and impact of comorbidities during the course of the disease will be the goal of this registry.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
500
Inclusion Criteria
  • Confirmed cardiac amyloidosis according to current standards
Exclusion Criteria
  • refusal to participate

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Cardiac AmyloidosisRoutine treatmentPatients with diagnosed cardiac amyloidosis being treated at Leipzig University Hospital.
Cardiac AmyloidosisRoutine diagnosticsPatients with diagnosed cardiac amyloidosis being treated at Leipzig University Hospital.
Primary Outcome Measures
NameTimeMethod
All-cause and cardiac mortality10 years

Mortality

Change in high-sensitivity cardiac troponin T over timeEvery 3-6 months over 10 years

Change in serum concentration of hs-cTnT

Rate of any hospitalizations10 years

Record of any clinical events requiring hospitalization

Change in left ventricular ejection fractionEvery 6-12 months over 10 years

Change in LVEF assessed by echocardiography or cardiac MRI

Change in left ventricular wall thicknessEvery 6-12 months over 10 years

Change in left ventricular wall thickness/ mass assessed by echocardiography or cardiac MRI

Change in extracellular volume valuesApprox. every 12 months over 10 years

Change in ECV assessed by cardiac MRI

Changes in medical treatment for heart failureEvery 3-6 months over 10 years

Changes in heart failure medication (i.e. diuretics, beta-blocker, renin-angiotensin system inhibitors, mineralocorticoid receptor antagonists, sodium glucose cotransporter type 2 inhibitors) as well as specific treatment for amyloidosis (e.g. tafamidis) is recorded.

Cumulative rate of patients with worsening heart failure10 years

Heart failure endpoint

Change in systolic arterial pressureEvery 6-12 months over 10 years

Change in sPAP assessed by echocardiography

Change in T1 valuesApprox. every 12 months over 10 years

Change in T1 values assessed by cardiac MRI

Change in N-Terminal Pro-B-Type Natriuretic Peptide over timeEvery 3-6 months over 10 years

Change in serum concentration of NT-proBNP

Secondary Outcome Measures
NameTimeMethod
Vital signs over timeEvery 3-6 months over 10 years

Blood pressure

Functional capacity over timeEvery 3-6 months over 10 years

Measured using 6 minute walk test

Clinical signs of congestion over timeEvery 3-6 months over 10 years

E.g. edema, jugular venous distension, crackles on lung auscultation

Prevalence and incidence of cardiac and non-cardiac comorbiditiesEvery 3-6 months over 10 years

Medical history and reports regarding any comorbidities and previous treatment will be assessed in detail at inclusion. Patients are asked for new comorbidities and new treatments at every visit.

New York Heart Association (NYHA) class over timeEvery 3-6 months over 10 years

As parameter of clinical status

Quality of life over timeEvery 3-6 months over 10 years

Measured via questionnaire (e.g. KCCQ)

Number of cardiovascular interventionsMonitoring continuously over 10 years

Indication, efficacy and safety of any cardiovascular intervention will be recorded, such as rate of pacemaker implantations, numbers of valve procedures (aortic valve implantation, mitral or tricuspid valve clipping), left atrial appendage occluder implantation, electrophysiological studies and ablation procedures

Trial Locations

Locations (1)

University Hospital Leipzig

🇩🇪

Leipzig, Saxony, Germany

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