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Cardiac Amyloidosis Registry Study

Conditions
Amyloidosis, Immunoglobulin Light-chain
Interventions
Other: Registry
Registration Number
NCT05174338
Lead Sponsor
Cedars-Sinai Medical Center
Brief Summary

This registry is a observational, multi-center study designed to collect data and analyze it retrospectively on patients with cardiac amyloidosis who have been evaluated and treated at major amyloid centers across the US and internationally between 1997 and 2025.

Detailed Description

Amyloidosis is a rare, multisystem disorder in which an insoluble protein is deposited in tissues, leading to organ dysfunction. Several proteins have been identified to potentially lead to amyloid cardiomyopathy (AC). Given the rare nature of these diseases, a large, multi-center effort to describe the characteristics of these patients and their outcomes with novel treatment modalities has not been established. (TBD) academic medical centers from the US and internationally will compile demographic, hemodynamic and organ-involvement data, as well as treatment strategies for AL and TTR amyloidosis.

This registry is an observational, multi-center study designed to collect data and analyze it retrospectively on patients with cardiac amyloidosis who have been evaluated and treated at major amyloid centers across the US and internationally between 1997 and 2025. It is expected that the total patient population will be approximately 5000 patients.

Recruitment & Eligibility

Status
ENROLLING_BY_INVITATION
Sex
All
Target Recruitment
5000
Inclusion Criteria
  • Established diagnosis of AL or TTR cardiomyopathy identified or treated within the timeframe
  • Specific to CSMC: If the individual provided consent while they were alive, and if sufficient information exists in their chart, their data will be included.
  • Information on deceased individuals may be included, but only with the appropriate approval from the external site IRB and/or according to the federal regulations for the protection of human subjects.
Exclusion Criteria
  • At Cedars-Sinai, records that specifically state not to be used in research will not be accessed. Patients who have enacted a No Research Flag or are noted as "Break the Glass" will not be included. For external sites, records that indicate No Research Flag or are noted as "Break the Glass" may be included based on institutional policies and appropriate approvals, as applicable.

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
AL and TTR amyloidosisRegistryimmunoglobulin light chain amyloidosis (AL) and transthyretin amyloidosis (ATTR)
Primary Outcome Measures
NameTimeMethod
Quantify incidence of complications from cardiac amyloidosis1997 - 2025

Determine incidence of arrhythmias (atrial fibrillation; ventricular arrhythmias) after diagnosis, renal dysfunction (rise in creatinine and development of end-stage renal disease), stroke, bleeding complications \[time frame 3 years\]

Quantify disease severity at diagnosis, progression and survival in patients with cardiac amyloidosis1997 - 2025

Clinical Outcomes: Disease severity at presentation, progression, and survival \[time frame 3 years\]. Severity and progression determined by change in NYHA Class, NT-ProBNP and troponin.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (23)

Johns Hopkins University School of Medicine

🇺🇸

Baltimore, Maryland, United States

University of Texas Southwestern Medical Center

🇺🇸

Dallas, Texas, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Boston Medical Center

🇺🇸

Boston, Massachusetts, United States

NYU Langone Health

🇺🇸

New York, New York, United States

University of California, San Francisco

🇺🇸

San Francisco, California, United States

University of Utah

🇺🇸

Salt Lake City, Utah, United States

UC San Diego Health, Sulpizio Cardiovascular Center

🇺🇸

La Jolla, California, United States

University of Arizona Sarver Heart Center

🇺🇸

Tucson, Arizona, United States

Scripps Health

🇺🇸

La Jolla, California, United States

Tufts Medical Center

🇺🇸

Boston, Massachusetts, United States

University of California Davis

🇺🇸

Sacramento, California, United States

MedStar Health and Vascular Institute/Georgetown University School of Medicine

🇺🇸

Washington, District of Columbia, United States

Weill Cornell Medicine

🇺🇸

New York, New York, United States

Washington University in St. Louis

🇺🇸

Saint Louis, Missouri, United States

Saint Luke's Hospital of Kansas City

🇺🇸

Kansas City, Missouri, United States

The Mount Sinai Hospital

🇺🇸

New York, New York, United States

Duke Health

🇺🇸

Durham, North Carolina, United States

Columbia University Irving Medical Center, Clinical Cardiovascular Research Laboratory for the Elderly (CUMC/CCRLE)

🇺🇸

New York, New York, United States

Penn Presbyterian Medical Center

🇺🇸

Philadelphia, Pennsylvania, United States

University of Texas Health Science Center at Houston

🇺🇸

Houston, Texas, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

University of Calgary

🇨🇦

Calgary, Alberta, Canada

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