Patient Characteristics and Treatment Patterns From Early Crizanlizumab Use in Real-world Setting: Preliminary Analysis From Select Sickle Cell Centers
- Conditions
- Sickle Cell Disease
- Registration Number
- NCT05833022
- Lead Sponsor
- Novartis Pharmaceuticals
- Brief Summary
This was a retrospective cohort study using secondary data from member sites of the National Alliance of Sickle Cell Centers (NASCC) with at least five patients who initiated crizanlizumab. Patients who were prescribed crizanlizumab were included in the cohort.
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- COMPLETED
- Sex
- All
- Target Recruitment
- 297
Not provided
Not provided
Study & Design
- Study Type
- OBSERVATIONAL
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Percentage of patients who received sickle cell disease treatment (use of hydroxyurea, l-glutamine, chronic transfusion therapy, and voxelotor) during treatment with crizanlizumab Up to 12 months Percentage of patients who received sickle cell disease treatment (use of hydroxyurea, l-glutamine, chronic transfusion therapy, and voxelotor) prior to treatment with crizanlizumab Up to 12 months
- Secondary Outcome Measures
Name Time Method Number of doses of crizanlizumab for patients who discontinued treatment with crizanlizumab Up to 24 months Number of sickle cell disease (SCD)-related hospitalizations Up to 24 months Number of patients who discontinued treatment with crizanlizumab Up to 24 months Reasons for early discontinuation of crizanlizumab treatment Up to 24 months Number of SCD-related emergency department (ED) visits Up to 24 months
Trial Locations
- Locations (11)
University of Alabama Birmingham
🇺🇸Birmingham, Alabama, United States
Cristiana Care
🇺🇸Wilmington, Delaware, United States
All Children's Hospital
🇺🇸Saint Petersburg, Florida, United States
Washington University of St. Louis
🇺🇸Saint Louis, Missouri, United States
Johns Hopkins University
🇺🇸Baltimore, Maryland, United States
Beth Israel Hospital
🇺🇸East Hanover, New Jersey, United States
Montefiore
🇺🇸New York, New York, United States
University of North Carolina
🇺🇸Chapel Hill, North Carolina, United States
University Hospital at Cleveland Medical Center
🇺🇸Cleveland, Ohio, United States
Ohio State University
🇺🇸Columbus, Ohio, United States
University of Texas (Houston)
🇺🇸Houston, Texas, United States