MedPath

Blockade of the Renin-angiotensin-aldosterone System in Patients with ARVD

Phase 2
Recruiting
Conditions
Arrhythmogenic Right Ventricular Dysplasia
Interventions
Registration Number
NCT03593317
Lead Sponsor
Hospices Civils de Lyon
Brief Summary

Arrhythmogenic right ventricular dysplasia (ARVD) is a rare cardiomyopathy characterized by the progressive replacement of cardiomyocytes by fatty and fibrous tissue in the right ventricle (RV). These infiltrations lead to cardiac electrical instability and ventricular arrhythmia.

Current treatment for ARVD is empirical and essentially based on treatment of arrhythmia. Thus, there is no validated treatment that will prevent the deterioration of the RV function in patients with ARVD.

The investigator's hypothesis is that the use of anti-fibrotic medications will prevent or at least reduce the deterioration of the RV function. The aim of this project is to evaluate the effect of spironolactone, a Potassium-sparing diuretic on ventricular myocardial remodeling and on arrhythmia burden in patients with ARVD.

The trial is a double-blind parallel multicenter prospective randomized phase II drug study. Patients will be randomized in the two groups: spironolactone or placebo. 13 centers in France will enroll the 120 patients (60 per group). Patients will be followed for 3 years (6 months, 1 year and 3 years) with all examinations (ECG, HA ECG, 24-hour Holter, trans-thoraciqc echocardiography (TTE), biological analyses) according to standard of care. A decrease in right and/or left ventricular deterioration and in arrhythmia burden are expected in ARVD patients treated with spironolactone. This reduction will improve the quality of life of patients and will reduce the number of hospitalizations and the risk of terminal heart failure.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
120
Inclusion Criteria
  • >18years old
  • Diagnosis of ARVD based on Task Force criteria. Two major criteria: 1 morphologic and one rhythmic or 1 major and 2 minor criteria established by the European Society of Cardiology/International Society and Federation of Cardiology.
  • Left Ventricular Ejection Fraction >40%
  • Written informed consent.
Exclusion Criteria

Patients under judicial protection.

  • Female patient who is pregnant or lactating, or is of child bearing potential (defined as a sexually mature woman not surgically sterilized or not post-menopausal for at least 24 consecutive months if ≤ 55 years or 12 months if > 55 years) and who did not agree to use highly effective methods of birth control throughout the study.
  • No health insurance.
  • Right heart failure patient (RV volume>150ml).
  • Spironolactone contraindication: hyperkalemia (K+>5 mmol/l), renal failure (DFGCréat>22 mL/min/1,73 m2), end-stage liver failure, Addison's Disease, hypersensitivity to spironolactone or to any of the excipients (patients with galactose intolerance, lapp lactase deficiency or glucose or galactose malabsorption syndrome), association with eplerenone, association with other hyperkalemic diuretics, association with potassium salts, not recommended in cirrhotic patients (natraemia<125 mmol/l) or in patients likely to present an acidosis.
  • Mandatory indication for a combination of ACE inhibitor and sartan or renin inhibitor (each authorized separately).
  • Acute phase of systemic disease.
  • Uncompensated hypothyroidism.
  • Acute hyperthyroidism.
  • Normal right ventricular volume.
  • Heart transplantation.
  • Swallowing disorders.
  • Participation in any other interventional clinical investigation that may have an impact on our study.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo groupPlacebo-
Spironolactone groupSpironolactone-
Primary Outcome Measures
NameTimeMethod
number of ventricular extrasystoles > 500 on 24h-Holter ECGat year 1
Right ventricle longitudinal strain measured by echocardiographyat year 1
Right ventricle infundibulum diameter measured by echocardiographyat year 1
Secondary Outcome Measures
NameTimeMethod
number of palpitationsat year 3
left ventricle volumes measured by echocardiographyat year 3

Morphologic criterion

number of ventricular extrasystoles on 24h-Holter ECGat year 1
number of sudden deathat year 3
number of ventricular tachycardiaat year 3
number of syncopeat year 3
Dosage of IL6 (Interleukin 6)at year 3

Quantification of inflammation

number of dyspneaat year 3
number of MACE (Major adverse cardiac events)at year 3
left ventricle diameters measured by echocardiographyat year 3

Morphologic criterion

number of thoracic painat year 3
number of hospital admissionsat year 3
left ventricle ejection fraction measured by echocardiographyat year 3

Morphologic criterion

aneurism measured by echocardiographyat year 3

Morphologic criterion

dyskinesia measured by echocardiographyat year 3

Morphologic criterion

sustained ventricular tachycardia on 24h Holter ECGat year 1

Rhythmic criterion

evolution of PR interval duration on ECGat year 1

Rhythmic criterion

late potentials measured with high amplification ECGat year 3

Rhythmic criterion

number of ventricular extrasystoles by stress testat year 3

Rhythmic criterion

Left ventricular global longitudinal strain measured by echocardiographyat year 1

Morphologic criterion

evolution of QRS width (50mm/s) on ECGat year 1

Morphologic criterion

Number of hospital admissions owing to clinical deteriorationat year 3
Evolution of telediastolic right ventricle volume measured by echocardiographyat year 3

according to the genotype of desmosome genes

arrhythmia burden measured by 24h Holter ECGat year 3

according to the genotype of desmosome genes

Dosage of MMP9 (Matrix metallopeptidase 9)at year 3

Quantification of fibrosis

Dosage of TIMP2 (Tissue Inhibitory MetalloProtease 2)at year 3

Quantification of fibrosis

number of ventricular extrasystoles on 24h Holter ECGat year 1

Rhythmic criterion

Evolution of functional symptoms by recording adverse eventsat year 3

Functional criteria

Dosage of TIMP1 (Tissue Inhibitory MetalloProtease 1)at year 3

Quantification of fibrosis

Dosage of IL8 (Interleukin 8)at year 3

Quantification of inflammation

Trial Locations

Locations (13)

CHU Amiens Picardie

🇫🇷

Amiens, France

Hôpital Cardiologique Louis Pradel

🇫🇷

Bron, France

Hôpital Gabriel Montpied

🇫🇷

Clermont-ferrand, France

CHU Dijon

🇫🇷

Dijon, France

Hôpital Michallon

🇫🇷

Grenoble, France

Hôpital de la Timone

🇫🇷

Marseille, France

Hôpital Arnaud de Villeneuve

🇫🇷

Montpellier, France

Hôpital Laennec

🇫🇷

Nantes, France

Groupe Hospitalo Universitaire Caremeau

🇫🇷

Nimes, France

Hôpital Pitié Salpetrière

🇫🇷

Paris, France

Hôpital de Haut-Lévêque

🇫🇷

Pessac, France

Nouvel Hôpital Civil

🇫🇷

Strasbourg, France

Hôpital Rangueil

🇫🇷

Toulouse, France

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