A Prospective Longitudinal Study in Adults With Multifocal Motor Neuropathy
- Conditions
- Multifocal Motor Neuropathy
- Registration Number
- NCT05988073
- Lead Sponsor
- argenx
- Brief Summary
This prospective longitudinal study will follow participants with Multifocal Motor Neuropathy over time and collect data on their clinical outcomes, quality of life, and use of health care resources. Participants will follow their regular visit schedule with their treating physician, except for an optional second visit occurring 7 to 14 days after the start of the study to collect biomarker data. No IMP will be administered.
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- ACTIVE_NOT_RECRUITING
- Sex
- All
- Target Recruitment
- 413
- Is at least the local legal age of consent for clinical studies when signing the ICF
- Is capable of providing signed informed consent and complying with protocol requirements
- Has an existing or new diagnosis of MMN made by a neuromuscular specialist or neurologist
- Is currently participating in any clinical study with an IMP
- Has other medical conditions that could affect the assessment of MMN
Study & Design
- Study Type
- OBSERVATIONAL
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method To characterize MMN patient profiles for participants up to 24 months To assess the MMN disease management and disease course up to 24 months To assess outcome measures specific to MMN disease and their evolution over time up to 24 months To estimate the burden of MMN on participants' quality of life up to 24 months To collect data on relevant disease biomarkers up to 24 months To estimate the economic burden for participants with MMN up to 24 months
- Secondary Outcome Measures
Name Time Method
Trial Locations
- Locations (113)
Universitatsklinikum Wurzburg
🇩🇪Wurzburg, Germany
Azienda Ospedaliero Universitaria Careggi
🇮🇹Firenze, Italy
Fondazione Serena Onlus - NeMO Brescia
🇮🇹Gussago, Italy
Azienda Ospedaliera Universitaria Gaetano Martino
🇮🇹Messina, Italy
Hospital de la Santa Creu i Sant Pau
🇪🇸Barcelona, Spain
Hospital Universitario de Basurto
🇪🇸Bilbao, Spain
Hospital Universitari de Bellvitge
🇪🇸L'Hospitalet de Llobregat, Spain
Centre Hospitalier de l'Universite de Montreal
🇨🇦Montreal, Canada
McGill University Health Centre - The Neuro (Montreal Neurological Institute-Hospital)
🇨🇦Montreal, Canada
Neuromuscular Clinical and Research Center
🇺🇸Phoenix, Arizona, United States
HonorHealth Neurology - Bob Bove Neuroscience Institute
🇺🇸Scottsdale, Arizona, United States
UCI Health - ALS and Neuromuscular Center
🇺🇸Orange, California, United States
Stanford Medicine Health Care - Stanford Neuroscience Health Center
🇺🇸Palo Alto, California, United States
The Neurology Group
🇺🇸Pomona, California, United States
Eisenhower Health - Rancho Mirage Medical Center
🇺🇸Rancho Mirage, California, United States
UC Davis Health - Lawrence J. Ellison Ambulatory Care Center
🇺🇸Sacramento, California, United States
UCSF Health - UCSF Medical Center
🇺🇸San Francisco, California, United States
University of Colorado - Anschutz Medical Campus
🇺🇸Aurora, Colorado, United States
YaleNewHavenHealth - Yale New Haven Hospital
🇺🇸New Haven, Connecticut, United States
MedStar Health - MedStar Georgetown University Hospital
🇺🇸Washington, District of Columbia, United States
Medsol Clinical Research Center Inc
🇺🇸Port Charlotte, Florida, United States
D&H National Research Centers - Tamarac Research Center
🇺🇸Tamarac, Florida, United States
Hospital Sisters Health System (HSHS) - St Elizabeth's Hospital
🇺🇸O'Fallon, Illinois, United States
The University of Kansas Health System - Landon Center on Aging
🇺🇸Kansas City, Kansas, United States
Rutgers University - Robert Wood Johnson Medical School
🇺🇸New Brunswick, New Jersey, United States
Columbia University Irving Medical Center - Neurological Institute of New York
🇺🇸New York, New York, United States
University of North Carolina - Chapel Hill
🇺🇸Chapel Hill, North Carolina, United States
Ohio State University Wexner Medical Center - Ohio State Martha Morehouse Outpatient Care
🇺🇸Columbus, Ohio, United States
Oregon Health and Science University (OHSU) Hospital - Marquam Hill Campus
🇺🇸Portland, Oregon, United States
Penn Medicine - Penn Medicine University City
🇺🇸Philadelphia, Pennsylvania, United States
Penn Medicine - Perelman Center for Advanced Medicine
🇺🇸Philadelphia, Pennsylvania, United States
University of Pittsburgh Medical Center
🇺🇸Pittsburgh, Pennsylvania, United States
Northwest Houston Neurology - Cypress
🇺🇸Cypress, Texas, United States
Royal Melbourne Hospital
🇦🇺Parkville, Australia
Gold Coast University Hospital
🇦🇺Southport, Australia
Princess Alexandra Hospital
🇦🇺Woolloongabba, Australia
Allgemeines Krankenhaus der Stadt Wien (AKH Wien)
🇦🇹Wien, Austria
Hopital Erasme
🇧🇪Bruxelles, Belgium
Universitair Ziekenhuis Antwerpen
🇧🇪Edegem, Belgium
Universitair Ziekenhuis Gent
🇧🇪Gent, Belgium
Universitair Ziekenhuis Brussel
🇧🇪Jette, Belgium
Universitair Ziekenhuis Leuven - Campus Gasthuisberg
🇧🇪Leuven, Belgium
L'hopital de la Citadelle - Site Citadelle
🇧🇪Liege, Belgium
Cliniques Universitaires Saint-Luc
🇧🇪Woluwe-Saint-Lambert, Belgium
Multiprofile Hospital for Active Treatment - Uni Hospital OOD
🇧🇬Panagyurishte, Bulgaria
Medical Center Medconsult Pleven OOD
🇧🇬Pleven, Bulgaria
Military Medical Academy - Military Hospital for Active Treatment Pleven
🇧🇬Pleven, Bulgaria
University Multiprofile Hospital for Active Treatment and Emergency Medicine N. I. Pirogov
🇧🇬Sofia, Bulgaria
London Health Sciences Centre - University Hospital
🇨🇦London, Canada
CHU de Quebec - Hopital de L'enfant Jesus
🇨🇦Quebec City, Canada
University of Saskatchewan - University of Saskatchewan College of Medicine
🇨🇦Saskatoon, Canada
Xiangya Hospital of Central South University
🇨🇳Changsha, China
The First Affiliated Hospital of Nanchang University
🇨🇳Nanchang, China
Huashan Hospital of Fudan University
🇨🇳Shangai, China
Fakultni nemocnice Brno - Areal Bohunice
🇨🇿Brno, Czechia
Fakultni nemocnice Hradec Kralove
🇨🇿Hradec Králové, Czechia
Aarhus Universitetshospital
🇩🇰Aarhus, Denmark
Rigshospitalet - Blegdamsvej
🇩🇰Copenhagen, Denmark
CHU Angers
🇫🇷Angers, France
CHU de Bordeaux - Hôpital Pellegrin
🇫🇷Bordeaux, France
CHU Brest - Hopital La Cavale Blanche
🇫🇷Brest, France
Hospices Civils de Lyon (HCL) - Hopital Pierre Wertheimer
🇫🇷Bron, France
Assistance Publique Hopitaux de Paris (AP-HP) - Hopital Bicetre
🇫🇷Le Kremlin-Bicetre, France
CHU Lille - Hopital Salengro
🇫🇷Lille, France
CHU de Limoges - CHU Dupuytren 1
🇫🇷Limoges, France
AP-HM - CHU Timone
🇫🇷Marseille, France
CHU de Nantes - Hotel Dieu
🇫🇷Nantes, France
CHU de Nice - Hopital Pasteur
🇫🇷Nice, France
Assistance Publique Hopitaux de Paris (AP-HP) - Hopital Pitie-Salpetriere
🇫🇷Paris, France
Universitatsklinikum Essen
🇩🇪Essen, Germany
Universitatsklinikum Giessen und Marburg - Campus Giessen
🇩🇪Gießen, Germany
Medizinische Hochschule Hannover
🇩🇪Hannover, Germany
St. Josefs- Krankenhaus Potsdam- Sanssouci
🇩🇪Potsdam, Germany
Universita degli Studi del Piemonte Orientale Amedeo Avogadro - Scuola di Medicina
🇮🇹Novara, Italy
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
🇮🇹Orbassano, Italy
Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone
🇮🇹Palermo, Italy
Istituto Neurologico Nazionale a Carattere Scientifico IRCCS
🇮🇹Pavia, Italy
Azienda Ospedaliero Universitaria Pisana - Ospedale Santa Chiara
🇮🇹Pisa, Italy
Azienda Ospedaliero Universitaria Sant'Andrea
🇮🇹Roma, Italy
Fondazione PTV Policlinico Tor Vergata
🇮🇹Roma, Italy
Teikyo University Hospital
🇯🇵Itabashi-ku, Japan
National Center of Neurology and Psychiatry
🇯🇵Kodaira-shi, Japan
Dokkyo Medical University Hospital
🇯🇵Mibu, Japan
Riga East Clinical University Hospital
🇱🇻Riga, Latvia
Pauls Stradins Clinical University Hospital
🇱🇻Riga, Latvia
Medicover Integrated Clinical Services (MICS) - Centrum Medyczne Bydgoszcz
🇵🇱Bydgoszcz, Poland
Wielospecjalistyczna Poradnia Lekarska Synapsis
🇵🇱Katowice, Poland
Specjalistyczne Gabinety Sp. z o.o.
🇵🇱Kraków, Poland
Michalski i Partnerzy Lekarze Spolka Partnerska
🇵🇱Kraków, Poland
SP ZOZ Szpital Uniwersytecki w Krakowie
🇵🇱Kraków, Poland
CLINIREM Sp z o.o.
🇵🇱Lublin, Poland
Rejdak Konrad Indywidualna Praktyka Lekarska
🇵🇱Lublin, Poland
Centrum Medyczne Hope Clinic
🇵🇱Lublin, Poland
ETG Network - ETG Neuroscience
🇵🇱Warsaw, Poland
Spitalul Clinic Judetean de Urgenta Sf. Apostol Andrei
🇷🇴Constanţa, Romania
Univerzitetski klinicki centar Srbije
🇷🇸Belgrade, Serbia
Univerzitetski klinicki centar Kragujevac
🇷🇸Kragujevac, Serbia
Hospital General Universitario Dr. Balmis
🇪🇸Alicante, Spain
Hospital Universitari Germans Trias i Pujol (HUGTP)
🇪🇸Badalona, Spain
Hospital Universitario Central de Asturias
🇪🇸Oviedo, Spain
Hospital Universitario de Navarra
🇪🇸Pamplona, Spain
Hospital Universitario de Donostia
🇪🇸San Sebastián, Spain
Sahlgrenska Universitetssjukhuset - MS - mottagning Sahlgrenska
🇸🇪Göteborg, Sweden
Karolinska Universitetssjukhuset - Huddinge
🇸🇪Huddinge, Sweden
North Bristol NHS Trust - Southmead Hospital Bristol
🇬🇧Bristol, United Kingdom
Lancashire Teaching Hospitals NHS Foundation Trust - Royal Preston Hospital
🇬🇧Fulwood, United Kingdom
NHS Great Glasgow and Clyde - Queen Elizabeth University Hospital
🇬🇧Glasgow, United Kingdom
Nottingham University Hospitals NHS Trust - Queen's Medical Centre
🇬🇧Nottingham, United Kingdom
Oxford University Hospitals NHS Foundation Trust - John Radcliffe Hospital
🇬🇧Oxford, United Kingdom
Northern Care Allicance NHS Foundation Trust - Salford Royal
🇬🇧Salford, United Kingdom
Sheffield Teaching Hospitals NHS Foundation Trust - Royal Hallamshire Hospital
🇬🇧Sheffield, United Kingdom
Somerset NHS Foundation Trust - Musgrove Park Hospital
🇬🇧Taunton, United Kingdom
Royal Cornwall Hospitals NHS Trust - Royal Cornwall Hospital
🇬🇧Truro, United Kingdom