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CMV Antiviral Prevention Strategies in D+R-Liver Transplants ("CAPSIL")

Phase 4
Completed
Conditions
Cytomegalovirus Infection
Interventions
Registration Number
NCT01552369
Lead Sponsor
National Institute of Allergy and Infectious Diseases (NIAID)
Brief Summary

This is a trial of preemptive therapy vs. prophylaxis for prevention of Cytomegalovirus (CMV) disease in R-D+ liver transplant patients. Subjects will be randomized within 10 days of transplant to receive in an open label design, either antiviral prophylaxis with valganciclovir, 900 mg orally once daily or preemptive therapy (weekly monitoring for CMV viremia by plasma PCR) for 100 days post-randomization with initiation of oral valganciclovir 900mg orally twice daily at onset of CMV viremia and continued until plasma PCR is negative on two consecutive weekly PCR tests). A minimum of 176 subjects will be enrolled in the study. The study duration is 7 years. The primary objective of this study is to compare prophylaxis versus preemptive therapy using valganciclovir for the prevention of CMV disease in R-/D+ liver transplant recipients.

Detailed Description

This is a prospective, randomized, multicenter trial of preemptive therapy vs. prophylaxis for prevention of Cytomegalovirus (CMV) disease in seronegative recipient- seropositive donor (R-D+) liver transplant patients.Subjects will be randomized within 10 days of transplant to receive in an open label design, either antiviral prophylaxis with valganciclovir 900 mg orally once daily or preemptive therapy for 100 days post-randomization with initiation of oral valganciclovir 900mg orally twice daily at onset of CMV viremia (monitored weekly) and continued until plasma PCR is negative on two consecutive weekly PCR tests. Study participants will be followed during the intervention period (100 days post randomization) and until 12 months post-transplant for CMV disease, toxicity, and clinical outcomes (opportunistic infections, rejection, graft loss and mortality). Drug safety labs will be assessed and recorded for the entire treatment period in both the prophylaxis and preemptive group. Re-transplantation and all-cause mortality will also be assessed at study closure and no longer than 5 years after enrollment. Additionally, the impact of the two CMV prevention strategies on CMV-specific cellular and humoral immune responses will be evaluated at 100 days after randomization, and 6 and 12 months post-transplant. A minimum of 176 subjects will be enrolled in the study. Allowing for over-enrollment to replace dropouts, up to 205 subjects may be enrolled to achieve the target enrollment of 176. Subjects will be randomized into one of the two groups in 1:1 ratio. The study duration is 7 years. The primary objective of this study is to compare prophylaxis versus preemptive therapy using valganciclovir for the prevention of CMV disease in R-/D+ liver transplant recipients. The secondary objectives are:1) to assess the two preventive strategies for clinical outcomes (major bacterial, fungal and non-CMV viral infections, rejection, graft loss and mortality) at one year post transplantation; 2) to assess the two preventive strategies for hematologic toxicity (assessment of neutropenia and receipt of hematopoietic growth factor during study days 1-107).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
205
Inclusion Criteria
  1. Be > / = 18 years of age.

  2. Have negative Cytomegalovirus (CMV) serology (confirmed within 6 months of transplant) and receive a liver from a donor with positive CMV serology (R-/D+).

  3. Have received their first orthotopic liver transplant (the transplanted liver may be deceased donor or live donor graft) within 10 days prior.

  4. Have absolute neutrophil count > 1000/µL at randomization.

    • If female, and not postmenopausal or surgically sterile, must have negative pregnancy test (serum or urine) within 48 hours prior to randomization and must also agree to use medically approved method of contraception. Acceptable methods include: barrier method, intrauterine device (hormonal or non-hormonal), oral hormonal contraceptives, abstinence for 100 days after randomization and 3 months after valganciclovir cessation.

    -- If male, and has not had a vasectomy, he must agree to practice barrier method of contraception for 100 days after randomization and 3 months after valganciclovir cessation.

  5. Subject or legally authorized representative has provided written informed consent.

Exclusion Criteria
  1. Currently enrolled in any interventional trial of an investigational therapeutic agent unless co-enrollment has been approved by study Principal Investigators (PIs) and the DMID prior to enrollment.
  2. Have hypersensitivity to acyclovir, ganciclovir or valganciclovir.
  3. Be breast-feeding mother.
  4. Have known Human immunodeficiency virus (HIV) infection (based on testing performed during the transplant evaluation process).
  5. Be undergoing multi organ transplant or have undergone prior organ transplant.
  6. Have expected life expectancy of less than 72 hours.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Preemptive TherapyValganciclovir900 mg of Valganciclovir given orally twice daily to Preemptive Therapy subjects upon detection of CMV viremia until plasma PCR is negative on two consecutive weekly PCR test. All dosages adjusted for renal dysfunction. n=88
ProphylaxisValganciclovir900 mg of Valganciclovir given orally once daily to subjects for 100 days post transplantation. All dosages adjusted for renal dysfunction. n=88
Primary Outcome Measures
NameTimeMethod
Incidence of Cytomegalovirus (CMV) Disease.365 days post-transplant

CMV disease as verified by an independent end point committee

Secondary Outcome Measures
NameTimeMethod
Neutropenia Less Than 500prior to day 107

ANC less than 500 while on valganciclovir

All-cause MortalityUp to 365 days post-transplant

Survival probability at 1 year

Incidence of Allograft RejectionUp to 365 days post-transplant

Number of subjects with allograft rejection

Graft LossUp to 365 days post-transplant

Incidence of graft loss (re-transplantation)

Late-onset CMV DiseaseUp to 365 days post-transplant

Incidence of late-onset CMV disease (occurring after 100 days post-randomization) as adjudicated by end point committee

Bacterial InfectionsUp to 365 days post-transplant

Incidence of bacterial opportunistic infections

Major Fungal InfectionsUp to 365 days post-transplant

Opportunistic fungal infections

Major Non-CMV Viral InfectionsUp to 365 days post-transplant

Incidence of non-CMV viral infections

NeutropeniaDay 1 through Day 107

Incidence of neutropenia less than 1000/µL while on valganciclovir treatment

Hematopoietic Growth FactorsDay 1 through Day 107

Hematopoietic growth factor receipt for ANC less than 500 during valganciclovir treatment.

Trial Locations

Locations (6)

Ronald Reagan University of California Los Angeles Medical Center

🇺🇸

Los Angeles, California, United States

Mayo Clinic, Rochester - Infectious Diseases

🇺🇸

Rochester, Minnesota, United States

Emory Clinic - Transplant Center

🇺🇸

Atlanta, Georgia, United States

University of Washington - Medicine

🇺🇸

Seattle, Washington, United States

University of Pittsburgh - Medicine - Infectious Diseases

🇺🇸

Pittsburgh, Pennsylvania, United States

Mount Sinai School of Medicine - Medicine - Infectious Diseases

🇺🇸

New York, New York, United States

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