MedPath

Clobazam in Patients With Lennox-Gastaut Syndrome

Phase 3
Completed
Conditions
Epilepsy
Epilepsy, Generalized
Seizures
Interventions
Registration Number
NCT00518713
Lead Sponsor
Lundbeck LLC
Brief Summary

The purpose of this study is to evaluate the safety and efficacy of clobazam as adjunctive therapy in the treatment of seizures which lead to drop attacks (drop seizures) in patients 2 to 60 years of age with Lennox-Gastaut Syndrome (LGS). Patients will be enrolled at approximately 65 sites in the U.S. and ex-US for up to 23 weeks. Patients will be randomly assigned to either a low, medium or high dose, or placebo. The study will include a baseline period, a titration period and a maintenance period. After the maintenance period, patients will either continue into an open-label extension study or enter the taper period with a final visit 1 week after the last dose.

Detailed Description

LGS poses a significant treatment challenge. No single antiepileptic drug (AED) provides satisfactory relief for all or most patients with LGS and a combination of treatments is often required. Even with combination therapy, many LGS patients show resistance to treatment. Adjunctive therapy with newer anticonvulsant medications has demonstrated efficacy for some patients, although polytherapy and high medication doses are often associated with unfavorable adverse event profiles.

More effective and better-tolerated treatment options are needed for this population of medically intractable epilepsy patients. Clobazam may provide an improved safety profile compared to other AEDs currently approved for the treatment of LGS and may have less hypotonia and drooling effects than other benzodiazepines.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
238
Inclusion Criteria
  • Patient must have been <11 years of age at the onset of LGS.
  • Patient must have LGS.
  • Patient must be on at least 1 AED.
  • Parent or caregiver must be able to keep an accurate seizure diary.
Exclusion Criteria
  • Etiology of patient's seizures is a progressive neurologic disease. Patients with tuberous sclerosis will not be excluded from study participation, unless there is a progressive tumor.
  • Patient has had an episode of status epilepticus within 12 weeks of baseline.
  • Patient has had an anoxic episode requiring resuscitation within 6 months of screening.
  • Patient has a clinically significant history of an allergic reaction or significant sensitivity to benzodiazepines.
  • Patient is taking more than 3 concurrent AEDs.
  • Patient has been on the ketogenic diet for less than 30 days prior to screening or suffers from frequent stooling.
  • If the patient has a Vagal Nerve Stimulator (VNS), the settings have not been stable for at least 30 days prior to screening.
  • Patient has taken corticotropins in the 6 months prior to screening.
  • Patient is currently taking long-term systemic steroids (excluding inhaled mediation for asthma treatment) or any other daily medication known to exacerbate epilepsy. An exception will be made of prophylactic medication, for example, for idiopathic nephrotic syndrome or asthma.
  • If the patient is taking felbamate, has been taking it for less than 1 year prior to screening.

Other protocol-defined inclusion and exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Clobazam Low DoseClobazam Low Dose-
Clobazam Medium DoseClobazam Medium Dose-
PlaceboPlacebo-
Clobazam High DoseClobazam High Dose-
Primary Outcome Measures
NameTimeMethod
Percent Reduction in Number of Drop Seizures (12-week Maintenance Period).4-week baseline period and 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Secondary Outcome Measures
NameTimeMethod
Percent Reduction in Number of Drop Seizures (First 4 Weeks of the 12-week Maintenance Period).4-week baseline period and the first 4 weeks of the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Percent Reduction in Number of Drop Seizures (Middle 4 Weeks of the 12-week Maintenance Period).4-week baseline period and the middle 4 weeks of the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Percent Reduction in Number of Drop Seizures (Last 4 Weeks of the 12-week Maintenance Period).4-week baseline period and the last 4 weeks of the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Percent of Patients Considered Treatment Responders Defined as Those With a >=25%, >=50%, >=75%, 100% Reduction in Drop Seizures (12-week Maintenance Period).4-week baseline period and the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Percent of Patients Considered Treatment Responders Defined as Those With a >=25%, >=50%, >=75%, 100% Reduction in Drop Seizures (First 4 Weeks of the 12-week Maintenance Period).4-week baseline period and the first 4 weeks of the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Percent of Patients Considered Treatment Responders Defined as Those With a >=25%, >=50%, >=75%, 100% Reduction in Drop Seizures (Middle 4 Weeks of the 12-week Maintenance Period).4-week baseline period and the middle 4 weeks of the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Percent of Patients Considered Treatment Responders Defined as Those With a >=25%, >=50%, >=75%, 100% Reduction in Drop Seizures (Last 4 Weeks of the 12-week Maintenance Period).4-week baseline period and the last 4 weeks of the 12-week maintenance period

Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

Tolerance4-week baseline period and first 4/first 8 weeks of the maintenance period

Study responders who have ≥50% reduction in their drop seizure rate during the first 4 or first 8 weeks of maintenance compared to the 4 week baseline period.

Investigator Global Evaluations of the Patient's Overall Change in Symptoms.Week 15

The physician was asked to rate the patient's overall change in symptoms and overall change in seizure activity and Quality of Life since the beginning of clobazam treatment by checking "very much improved", "much improved", "minimally improved", "no change", "minimally worse", "much worse", or "very much worse".

Parent/Caregiver Global Evaluations of the Patient's Overall Change in Symptoms.Week 15

The parent/caregiver was asked to rate the patient's overall change in symptoms and overall change in seizure activity and Quality of Life since the beginning of clobazam treatment by checking "very much improved", "much improved", "minimally improved", "no change", "minimally worse", "much worse", or "very much worse".

Trial Locations

Locations (53)

Children's Memorial Hospital

🇺🇸

Chicago, Illinois, United States

Baylor College of Medicine Pediatric Neurology

🇺🇸

Houston, Texas, United States

Jefferson Epilepsy Center

🇺🇸

Philadelphia, Pennsylvania, United States

St. John's Medical College Hospital

🇮🇳

Bangalore, Karnataka, India

University of Kentucky, Kentucky Clinic, Department of Neurology

🇺🇸

Lexington, Kentucky, United States

Children's Medical Center at UT Southwestern-Dallas

🇺🇸

Dallas, Texas, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

St. Joseph's Regional Medical Center

🇺🇸

Paterson, New Jersey, United States

Medical College of Georgia

🇺🇸

Augusta, Georgia, United States

The Comprehensive Epilepsy Care Center for Children and Adults

🇺🇸

Chesterfield, Missouri, United States

Pediatric Neurology of Idaho Children's Specialty Center

🇺🇸

Boise, Idaho, United States

Deenanath Mangeshkar Hospital and Research Center

🇮🇳

Erandawane, Pune, India

Robert Wood Johnson University Hospital

🇺🇸

New Brunswick, New Jersey, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

LSU Health Sciences Center

🇺🇸

Shreveport, Louisiana, United States

University of Chicago Medical Center

🇺🇸

Chicago, Illinois, United States

Vitebsk Regional Diagnostic Center

🇧🇾

Vitebsk, Belarus

Cook Children's Health Care System

🇺🇸

Fort Worth, Texas, United States

The Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

University Neurology, Inc.

🇺🇸

Cincinnati, Ohio, United States

Royal Melbourne Hospital Department of Neurology

🇦🇺

Melbourne, Victoria, Australia

Maulana Azad Medical College and Associated Lok Nayak Govind Ballabh Pant Hospitals and Guru Nanak Eye centre

🇮🇳

New Delhi, Delhi, India

University of Rochester Medical Center

🇺🇸

Rochester, New York, United States

K. S. Hedge Medical Academy

🇮🇳

Mangalore, Karnataka, India

P.D. Hinduja National Hospital Medical Research Centre

🇮🇳

Mumbai, India

Dr. Kamakshi Memorial Hospital

🇮🇳

Chennai, Tamilnadu, India

Institute of Human Behaviour and Allied Sciences

🇮🇳

Delhi, New Delhi, India

Christian Medical College

🇮🇳

Ludhiana, Punjab, India

Apollo Gleneagles Hospitals

🇮🇳

Kolkata, West Bengal, India

Chhatrapati Sahu Ji Maharaj Medical University

🇮🇳

Lucknow, Uttra Pradesh, India

Kaunas University of Medicine Hospital

🇱🇹

Kaunas, Lithuania

Mid-Atlantic Epilepsy and Sleep Center

🇺🇸

Bethesda, Maryland, United States

Phoenix Children's Hospital

🇺🇸

Phoenix, Arizona, United States

The Children's Hospital

🇺🇸

Aurora, Colorado, United States

Pediatric Epilepsy & Neurology Specialists

🇺🇸

Tampa, Florida, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

University of Alabama at Birmingham

🇺🇸

Huntsville, Alabama, United States

Childrens Hospital Los Angeles

🇺🇸

Los Angeles, California, United States

St. Joseph's Hospital and Medical Center

🇺🇸

Phoenix, Arizona, United States

University of South Florida

🇺🇸

Tampa, Florida, United States

Child Neurology Center of NW FL

🇺🇸

Pensacola, Florida, United States

Pediatric Neurology and Epilepsy Center

🇺🇸

Loxahatchee, Florida, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Minnesota Epilepsy Group

🇺🇸

St. Paul, Minnesota, United States

Dartmouth-Hitchcock Medical Center

🇺🇸

Lebanon, New Hampshire, United States

Clinical Research Center of New Jersey (CRCNJ)

🇺🇸

Voorhees, New Jersey, United States

Strategic Health Evaluators

🇦🇺

Chatswood, New South Wales, Australia

Austin & Repatriation Hospital (Austin Health) Epilepsy Research Centre

🇦🇺

Melbourne, Victoria, Australia

Neurology Center

🇮🇳

Ahmedabad, Gujarat, India

Malikatta Neuro Center

🇮🇳

Mangalore, Karnataka, India

Jaslok Hospital & Research Centre

🇮🇳

Mumbai, Maharashtra, India

KEM Hospital & Research Centre

🇮🇳

Pune, Maharashtra, India

UTMG Pediatric Neurology

🇺🇸

Memphis, Tennessee, United States

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