MedPath

Acthar Gel for Active Systemic Lupus Erythematosus (SLE)

Phase 4
Completed
Conditions
Lupus Erythematosus, Systemic
Interventions
Drug: Placebo Gel
Registration Number
NCT02953821
Lead Sponsor
Mallinckrodt
Brief Summary

This trial is to study Acthar Gel in participants with active systemic lupus erythematosus (SLE).

The doctor will assign eligible patients to one of two groups (like flipping a coin).

Participants will receive the treatment assigned to their group for 24 weeks:

* Acthar Gel

* Placebo Gel, which looks like Acthar Gel, but has no medicine in it.

The doctor or his staff will take measurements and ask questions to:

* see how well the gel is working

* see how safe it is for patients with SLE

Detailed Description

This trial was initiated (started recruiting) in October 2016, but first patient was not enrolled (randomized) until December, 2016.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
172
Inclusion Criteria

To be eligible to participate in this trial, a patient must:

  • Have a diagnosis of SLE according to 4 of the American College of Rheumatology revised criteria

  • Have active SLE

  • Have moderate to severe rash and/or arthritis as demonstrated by BILAG-2004 score A or B in the mucocutaneous and/or musculoskeletal body systems at both Screening and Randomization Visits

  • Have a documented history or screening result of

    1. positive antinuclear antibody (ANA), OR
    2. elevated anti-dsDNA or extractable nuclear antigen (ENA) antibodies
  • Have been on prednisone (or prednisone equivalent) before the screening visit:

    1. at least 8 weeks, and
    2. at a stable dose of 7.5 mg to 30 mg for at least 4 weeks

Exclusion criteria:

A patient is not eligible to participate if he/she:

  • Has a history of sensitivity to adrenocorticotropic hormone (ACTH) preparations or porcine products
  • Has active lupus nephritis
  • Has active central nervous system (CNS) manifestations of SLE
Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Acthar GelActhar GelParticipants receive Acthar Gel every other day for 4 weeks, and then twice per week for 20 weeks
Placebo GelPlacebo GelParticipants receive Placebo Gel every other day for 4 weeks, and then twice per week for 20 weeks
Primary Outcome Measures
NameTimeMethod
British Isles Lupus Assessment Group 2004 (BILAG 2004)Baseline, Week 16, Week 24

BILAG records disease activity occurring over the past 4 weeks, and is used to determine whether different course of treatment is required. The BILAG-2004 index covers 97 signs/symptoms across 9 organ systems. Each question is answered as 0-not present, 1-improving, 2-same, 3-worse, or 4-new.

The BILAG-2004 index categorizes disease activity in each organ system into five different levels from A to E. Grade A represents very active disease, Grade B represents moderate disease activity, Grade C indicates mild stable disease, and grade D implies no disease activity, but suggests the organ system had previously been affected. Grade E indicates no current or previous disease activity. A score is applied to each grade of each organ system using coding scheme of A=12, B=8, C=1, and D/E=0 and is summarized as a total score ranging 0-108. Higher scores indicate more severe disease activity.

Number of Participants With at Least a 4 Point Change From Baseline in Systemic Lupus Erythematosus Disease Activity Index-2000 (SLEDAI-2K)Week 16, Week 24

The SLEDAI-2K is a modified version of a composite score based on the presence or absence of clinical signs, clinical symptoms, and immunologic laboratory results taken within 10 days of the evaluations. Each of the descriptors has a weighted score and the total score of SLEDAI-2K is the sum of all 24 descriptor scores. The total SLEDAI-2K score falls between 0 and 105, with higher scores representing higher disease activity. Decrease from baseline indicates improvement.

Physician's Global Assessment (PGA)Baseline, Week 16, Week 24

PGA is a 100 mm visual analogue scale where higher scores indicate more severe disease activity. Lower scores indicate improvement.

Secondary Outcome Measures
NameTimeMethod
Number of Participants With Severe Flare, Based on the SELENA Flare Index (SFI) at Week 16Week 16

Among some adults, having a period of SLE symptoms-called flares-may happen every so often, sometimes even years apart, and go away at other times-called remission. The SFI categorizes SLE flares as mild, moderate or severe.

Mean Cutaneous Lupus Erythematosus Disease Area and Severity Score- Activity (CLASI) Total Activity Scoreat Baseline and Weeks 4, 8, and 16

The CLASI total activity score reflects ongoing inflammation that can be treated, with points given for the presence of erythema, scale, mucous membrane lesions, recent hair loss, and inflammatory alopecia. Mild, moderate, and severe disease correspond with CLASI activity score ranges of 0 to 9, 10 to 20, and 21 to 70, respectively. Higher scores indicate more disease activity, lower scores indicate improvement.

Mean Number of Swollen or Tender Joints on the 28-Joint Countat Baseline and at Weeks 4, 8, 12 and 16

The 28 Joint Count includes assessment of swelling and tenderness in the shoulders, elbows, wrists, metacarpophalangeal joints, proximal interphalangeal joints and knees. The investigator counts how many of the 28 joints are swollen or tender at the given week.

Number of Participants With Decrease in Prednisone Dose to < 7.5 mg/Day at Week 20 and Week 24Week 20, Week 24

Trial Locations

Locations (39)

Center for Rheumatology Immunology and Arthritis

🇺🇸

Fort Lauderdale, Florida, United States

Sun Research Institute

🇺🇸

San Antonio, Texas, United States

IBIOMED Research Unit Aguascalientes

🇲🇽

Aguascalientes, Mexico

Consultorio de Reumatología

🇲🇽

México, Mexico

Centro de Alta Especialidad en Reumatologia e Investigación del Potosí, SC

🇲🇽

San Luis Potosí, Mexico

C.V. Mehta MD Medical Corporation

🇺🇸

Hemet, California, United States

Paramount Medical Research & Consulting

🇺🇸

Middleburg Heights, Ohio, United States

Biomedica Research Group

🇨🇱

Santiago, Chile

San Marcus Research Clinic

🇺🇸

Miami, Florida, United States

Office of George Timothy Kelly MD

🇺🇸

Las Vegas, Nevada, United States

Centro Especializado en Investigación Clínica

🇲🇽

Boca Del Río, Mexico

Inland Rheumatology Clinical Trials

🇺🇸

Upland, California, United States

West Tennessee Physicians' Alliance

🇺🇸

Jackson, Tennessee, United States

NewYork-Presbyterian Columbia University Medical Center

🇺🇸

New York, New York, United States

DJL Clinical Research

🇺🇸

Charlotte, North Carolina, United States

Altoona Center for Clinical Research

🇺🇸

Duncansville, Pennsylvania, United States

Consultorios Médicos Dr. Catalán Pellet

🇦🇷

Buenos Aires, Argentina

Centro Medico Privado de Reumatología

🇦🇷

Tucumán, Argentina

Advanced Pharma CR

🇺🇸

Miami, Florida, United States

Office of Ramesh C. Gupta, MD

🇺🇸

Memphis, Tennessee, United States

Unidad de Investigación de las Enfermedades Reumáticas

🇲🇽

Ciudad de mexico, Mexico

Antiguo Hospital Civil de Guadalajara Fray Antonio Alcalde

🇲🇽

Guadalajara, Jalisco, Mexico

Centro Integral de Reumatologia

🇲🇽

Mexico, Mexico

Centro Peninsular de Investigacion Clinica S.C.P.

🇲🇽

Mérida, Mexico

Centro de Estudios Clínicos y Especialidades Médicas

🇲🇽

Monterrey, Mexico

SMIQ

🇲🇽

Queretaro, Mexico

Hospital de Apoyo Maria Auxiliadora

🇵🇪

San Juan De Miraflores, Peru

Millennium Research

🇺🇸

Ormond Beach, Florida, United States

Arthritis & Rheumatology Center of Oklahoma

🇺🇸

Oklahoma City, Oklahoma, United States

Accurate Clinical Research

🇺🇸

Houston, Texas, United States

Instituto de Investigaciones Aplicadas a la Neurociencia A.C.

🇲🇽

Durango, Mexico

Accelerium Clinical Research

🇲🇽

Monterrey, Mexico

Phylasis Clinicas Research S de RL de CV

🇲🇽

Cuautitlan Izcalli, Mexico

Köhler and Milstein Research

🇲🇽

Mérida, Mexico

Investigacion Biomedica para el Desarrollo de Farmacos S.A. de C.V.

🇲🇽

Zapopan, Mexico

Clinica Vesalio

🇵🇪

San Borja, Peru

Investigaciones Clinicas S.A.C. del Instituto de Ginecologia y Reproduccion

🇵🇪

Lima, Peru

Hospital Nacional Cayetano Heredia

🇵🇪

San Martin De Porres, Peru

Aprillus Asistencia e Investigación

🇦🇷

Buenos Aires, Argentina

© Copyright 2025. All Rights Reserved by MedPath