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Special Use-results Surveillance on Long Term Use of Sogroya® in Children With Short Stature Due to Growth Hormone Deficiency Where Epiphysial Discs Are Not Closed

Conditions
Growth Hormone Deficiency in Children
Interventions
Registration Number
NCT06109935
Lead Sponsor
Novo Nordisk A/S
Brief Summary

The purpose of the study is to investigate the safety and effectiveness of Sogroya® in children with short stature due to growth hormone deficiency where epiphysial discs are not closed under real-world clinical practice in Japan. The study will last for about 1 year (at shortest) to 3 years (at longest) depending on when the participant takes part in the study. The participant will be asked to answer questionnaire(s) about how they feel about the growth hormone (GH) product treatment once during the study (at about 3 months after starting the Sogroya® treatment) and about 3 months after starting the Sogroya® treatment.

Detailed Description

Not available

Recruitment & Eligibility

Status
ENROLLING_BY_INVITATION
Sex
All
Target Recruitment
200
Inclusion Criteria
  1. Signed consent obtained before any study-related activities (study-related activities are any procedure related to recording of data according to the protocol).
  2. The decision to initiate treatment with commercially available Sogroya® has been made by the patient/Legally Acceptable Representative (LAR) and the treating physician before and independently from the decision to include the patient in this study. Both GH treatment naïve and non-naïve children are eligible.
  3. Male or female age 0 to 18 years (exclusive) at the time of signing informed consent.
  4. Diagnosis with short stature due to GHD where epiphysial discs are not closed according to local normal clinical practice.
Exclusion Criteria
  1. Previous participation in this study. Participation is defined as having given informed consent in this study.

  2. Treatment with any investigational drug within 30 days prior to baseline (the starting date of Sogroya® treatment).

  3. Mental incapacity, unwillingness or language barriers precluding adequate understanding or cooperation.

  4. Contraindication described in approved product labelling in Japan.

    1. Patients with hypersensitivity to the active substance or to any of the excipients
    2. Patients with malignant tumour
    3. Female patients who are either pregnant or likely to be pregnant

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Children with GHDSomapacitanParticipants will be treated with commercially available Sogroya® according to routine clinical practice at the discretion of the treating physician. Administration will be according to the approved product labelling. The decision to treat a participant with Sogroya® is made at the treating physician's discretion before and independently from the decision to include the patient in this study.
Primary Outcome Measures
NameTimeMethod
Number of adverse reactions (AR)From baseline (week 0) to end of study (up to 156 weeks)

Measured as count of reactions.

Secondary Outcome Measures
NameTimeMethod
Number of adverse events (AEs)From baseline (week 0) to end of study (up to 156 weeks)

Measured as count of events.

Number of serious adverse reactions (SARs)From baseline (week 0) to end of study (up to 156 weeks)

Measured as count of reactions.

Change in height velocity (HV)Every 12 months from baseline (week 0) to end of study (up to 156 weeks)

Measured in centimeter (cm)/year.

Change in height standard deviation score (HSDS)Every 12 months from baseline (week 0) to end of study (up to 156 weeks)
Number of serious adverse events (SAEs)From baseline (week 0) to end of study (up to 156 weeks)

Measured as count of events.

Change in ratio of bone age/chronological ageEvery 12 months from baseline (week 0) to end of study (up to 156 weeks)
Growth hormone device assessment tool (G-DAT)At 12 weeks

Measured as count of patients choosing the individual response category. G-DAT is a questionnaire to gather information on how they feel about the GH product device assessed as "very easy", "easy", "neither difficult or easy", "difficult" or "very difficult" where "very easy" is best and "very difficult" is worst.

Growth hormone patient preference questionnaire (GH-PPQ)At 12 weeks

Measured as count of patients choosing the individual response category. GH-PPQ is a disease specific questionnaire which measures the patient's growth hormone treatment preference.

Change in bone ageEvery 12 months from baseline (week 0) to end of study (up to 156 weeks)

Measured in years.

Change in height velocity standard deviation score (HVSDS)Every 12 months from baseline (week 0) to end of study (up to 156 weeks)
Change in insulin-like growth factor-I standard deviation score (IGF-I SDS)Every 12 months from baseline (week 0) to end of study (up to 156 weeks)

Measured as score ranging from -10 to +10. Negative scores indicated a IGF-I below the mean IGF-I for a child with the same age and gender, whereas positive scores indicated a IGF-I above the mean IGF-I for a child with the same age and gender. For participants with low IGF-I SDS at baseline, a positive change from baseline in IGF-I SDS indicated a better outcome.

Trial Locations

Locations (47)

Asahikawa Medical Univ. Hospital, Pediatrics

🇯🇵

Asahikawa, Hokkaido, Japan

Beppu Medical Center

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Beppu-shi, Oita-ken, Japan

Fukuoka University Hospital

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Fukuoka-shi, Fukuoka-ken, Japan

Kurume University Hospital, Pediatrics

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Fukuoka, Japan

Kyushu University Hospital

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Fukuoka-shi, Fukuoka, Japan

Gifu University Hospital

🇯🇵

Gifu, Japan

Ota Memorial Hospital_Pediatrics

🇯🇵

Gunma, Japan

Kato Clinic

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Hachioji-shi, Tokyo-to, Japan

Hamamatsu University Hospital

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Hamamatsu-shi, Shizuoka, Japan

Hello Clinic

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Higashimatsuyama-shi, Saitama-ken, Japan

Japanese Red Cross Society Himeji Hospital

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Himeji-shi, Hyogo-ken, Japan

Hyogo prefectural kobe children's hospital

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Hyogo, Japan

Sunsun Kodomo Clinic

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Ichikawa-shi, Chiba-ken, Japan

Iwate Medical University Hospital

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Iwate, Japan

Fukushima Seishi Ryougoen

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Iwaki-shi, Fukushima-ken, Japan

Shimane University Hospital_Pediatrics

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Izumo-shi, Shimane-ken, Japan

University Hospital Kyoto Prefectual University of Medicine

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Kamigyo-ku, Kyoto, Japan

Odawara Municipal Hospital

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Kanagawa, Japan

Naha City Hospital

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Naha-shi, Okinawa, Japan

Nippon Medical School Musashikosugi Hospital

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Kawasaki-shi, Kanagawa-ken, Japan

Hospital of the University of Occupational And Environmental Health Japan, Pediatrics

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Kitakyusyu-shi, Fukuoka, Japan

Ayabe City Hospital

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Kyoto, Japan

Haga Red Cross Hospital

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Moka-shi, Tochigi-ken, Japan

Nagoya City University Hospital, Pediatric

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Nagoya, Aichi, Japan

Kodomohamirai Morioka Kodomo Clinic

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Morioka-shi, Iwate-ken, Japan

Hyogo Medical University Hospital_Pediatrics

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Nishinomiya-shi, Hyogo-ken, Japan

Nara Prefecture General Medical Center

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Nara-shi, Nara, Japan

Nara Medical University Hospital_Pediatrics

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Nara, Japan

Aichi Children's Health and Medical Center

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Obu-shi, Aichi, Japan

Chibana Clinic

🇯🇵

Okinawa, Japan

Osaka City General Hospital

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Osaka, Japan

Osaka University Hospital

🇯🇵

Osaka, Japan

Saiseikai Suita Hospital

🇯🇵

Osaka, Japan

Kibounomori Clinic

🇯🇵

Oosakashi, Japan

Yasuhara Children's Clinic

🇯🇵

Osaka, Japan

Osaka Women's and Children's Hospital

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Osaka, Japan

Kojiya Kodomo clinic

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Ota-ku, Tokyo-to, Japan

Okubo Kids Clinic

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Ozu-shi, Ehime-ken, Japan

Sakai Smile Kids Clinic

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Sashima-gun, Ibaraki-ken, Japan

Tanaka Growth Clinic

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Tokyo, Japan

Toyohashi Municipal Hospital

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Toyohashi-shi, Aichi-ken, Japan

Murakami Pediatric and Allergy clinic

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Toyama-shi, Toyama-ken, Japan

Ehime University Hospital

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Toon-shi, Ehime, Japan

University of the Ryukyus Hospital

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Nakagami-gun, Okinawa-ken, Japan

JR Sendai Hospital

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Sendai-shi, Miyagi-ken, Japan

Hamamatsu Medical Center

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Shizuoka, Japan

Ikeda Pediatrics Clinic

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Yamagata-shi, Yamagata-ken, Japan

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