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avalglucosidase alfa Special Drug Use Investigation for patients with pompe disease

Not Applicable
Recruiting
Conditions
Pompe disease
Registration Number
JPRN-UMIN000047301
Lead Sponsor
Sanofi K.K.
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
50
Inclusion Criteria

Not provided

Exclusion Criteria

-Individuals participating in or enrolling in other clinical trials involving therapeutic interventions of Nexviazyme -Those with off-label use of Nexviazyme

Study & Design

Study Type
Observational
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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